E-LIB Suche - Ergebnisse für: Mueller-Felber, W.

1

Effects of gene replacement therapy with resamirigene bilpa..:

Lawlor, Michael W. ; Schoser, Benedikt ; Margeta, Marta...
eBioMedicine. 99 (2024) - p. 104894 , 2024

Link: https://doi.org/10.1016/..

2

Efficient ex vivo expansion of conserved element vaccine-sp..:

Dross, Sandra ; Venkataraman, Rasika ; Patel, Shabnum...
Frontiers in Immunology. 14 (2023) - p. , 2023

Link: https://doi.org/10.3389/..

3

P206 Impaired neurodevelopment in children with 5q-SMA - 2 ..:

Kölbel, H. ; Kopka, M. ; Modler, L....
Neuromuscular Disorders. 33 (2023) - p. S86 , 2023

Link: https://doi.org/10.1016/..

4

Initial Results from Stanford Children's Fanconi Anemia Cli..:

Agarwal, Rajni ; Bertaina, Alice ; Nofal, Rofida...
Transplantation and Cellular Therapy. 29 (2023) 2 - p. S163-S164 , 2023

Link: https://doi.org/10.1016/..

5

Comparative immunogenicity of an mRNA/LNP and a DNA vaccine..:

Valentin, Antonio ; Bergamaschi, Cristina ; Rosati, Margherita...
Frontiers in Immunology. 13 (2022) - p. , 2022

Link: https://doi.org/10.3389/..

6

INCEPTUS Natural History, Run-in Study for Gene Replacement..:

Dowling, James J. ; Müller-Felber, Wolfgang ; Smith, Barbara K....
Journal of Neuromuscular Diseases. 9 (2022) 4 - p. 503-516 , 2022

Link: https://doi.org/10.3233/..

7

VP.17 Long-term effect of nusinersen treatment on motor, re..:

Pechmann, A. ; Behrens, M. ; Bernert, G....
Neuromuscular Disorders. 32 (2022) - p. S63-S64 , 2022

Link: https://doi.org/10.1016/..

8

O.13 Givinostat in DMD: results of the Epidys Study:

Mercuri, E. ; Vilchez, J. ; Boespflug-Tanguy, O....
Neuromuscular Disorders. 32 (2022) - p. S95-S96 , 2022

Link: https://doi.org/10.1016/..

9

O.06 Long term outcomes for X-Linked myotubular Myopathy (X..:

Shieh, P. ; Kuntz, N. ; Dowling, J....
Neuromuscular Disorders. 32 (2022) - p. S44 , 2022

Link: https://doi.org/10.1016/..

10

A recurrent single-amino acid deletion (p.Glu500del) in the..:

Bader, Ingrid ; Freilinger, M. ; Landauer, F....
Orphanet Journal of Rare Diseases. 17 (2022) 1 - p. , 2022

Link: https://doi.org/10.1186/..

11

CLINICAL TRIAL HIGHLIGHTS:

Shieh, P. ; Kuntz, N. ; Dowling, J....
Neuromuscular Disorders. 31 (2021) - p. S47 , 2021

Link: https://doi.org/10.1016/..

12

A Randomized, Double-Blind, Placebo-Controlled, Global Phas..:

Finkel, Richard S. ; McDonald, Craig M. ; Lee Sweeney, H....
Journal of Neuromuscular Diseases. 8 (2021) 5 - p. 769-784 , 2021

Link: https://doi.org/10.3233/..

13

Neugeborenenscreening auf spinale Muskelatrophie; Newborn s..:

Müller-Felber, W. ; Vill, K. ; Schwartz, O....
Monatsschrift Kinderheilkunde. 172 (2021) 7 - p. 595-600 , 2021

Link: https://doi.org/10.1007/..

14

Validation of the TORSAFUF score in diagnosis of spermatic ..:

Plassais, C. ; Bentellis, I. ; Pinar, U....
European Urology. 79 (2021) - p. S1235-S1236 , 2021

Link: https://doi.org/10.1016/..

15

Impact of testicular torsion on fertility and erectile dysf..:

Berchiche, W. ; Sbizzera, M. ; Lannes, F....
European Urology. 79 (2021) - p. S714 , 2021

Link: https://doi.org/10.1016/..