Adams, David ; Tournev, Ivailo L ; Taylor, Mark S... https://discovery.ucl.ac.uk/id/eprint/10152616/1/Efficacy%20and%20safety%20of%20vutrisiran%20for%20patients%20with%20hereditary%20transthyretin%20mediated%20amyloidosis%20with%20polyneuropathy%20a%20randomized%20clinical%20trial.pdf.
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2022