Samulski, Richard Jude
230  results:
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1

Rationally engineered novel AAV capsids for intra-articular..:

Li, Wenjun ; Feng, Susi Liu ; Herrschaft, Lizette..
Molecular Therapy - Methods & Clinical Development.  32 (2024)  1 - p. 101211 , 2024
 
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2

Nicholas Muzyczka, PhD:

Berns, Kenneth I. ; Byrne, Barry J. ; Flotte, Terence R...
Molecular Therapy.  31 (2023)  3 - p. 607 , 2023
 
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4

Evaluation of an AAV9-mini-dystrophin gene therapy candidat..:

Le Guiner, Caroline ; Xiao, Xiao ; Larcher, Thibaut...
Molecular Therapy - Methods & Clinical Development.  30 (2023)  - p. 30-47 , 2023
 
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10

A first-in-human phase 1 clinical gene therapy trial for th..:

Alvisi, Monica ; Henry, Timothy ; Chung, Eugene...
Journal of Molecular and Cellular Cardiology.  173 (2022)  - p. S113 , 2022
 
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12

AAV vectors: The Rubik's cube of human gene therapy:

Pupo, Amaury ; Fernández, Audry ; Low, Siew Hui...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC9734031/.  , 2022
 
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