Sframeli, Maria
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7

Onasemnogene abeparvovec in spinal muscular atrophy: predic..:

Marika Pane ; Beatrice Berti ; Anna Capasso...
http://www.sciencedirect.com/science/article/pii/S2589537023001748.  , 2023
 
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Molecular analysis of SMARD1 patient-derived cells demonstr..:

Taiana, Michela ; Govoni, Alessandra ; Salani, Sabrina...
Journal of Neurology, Neurosurgery & Psychiatry.  93 (2022)  8 - p. 908-910 , 2022
 
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13

Nusinersen efficacy data for 24‐month in type 2 and 3 spina..:

Pane, Marika ; Coratti, Giorgia ; Pera, Maria Carmela...
Annals of Clinical and Translational Neurology.  9 (2022)  3 - p. 404-409 , 2022
 
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