E-LIB Suche - Ergebnisse für: Mercuri, E

1

P75 Revised Hammersmith Scale item achievement by functiona..:

Ramsey, D. ; Stimpson, G. ; Wolfe, A....
Neuromuscular Disorders. 33 (2023) - p. S135 , 2023

Link: https://doi.org/10.1016/..

2

P196 Age at loss of ambulation in patients with DMD from th..:

Mercuri, E. ; Muntoni, F. ; Buccella, F....
Neuromuscular Disorders. 33 (2023) - p. S143 , 2023

Link: https://doi.org/10.1016/..

3

P198 Updated demographics and safety data from patients wit..:

Muntoni, F. ; Buccella, F. ; Desguerre, I....
Neuromuscular Disorders. 33 (2023) - p. S143-S144 , 2023

Link: https://doi.org/10.1016/..

4

P35 Two-year clinical outcomes with fordadistrogene movapar..:

Shieh, P. ; Butterfield, R. ; Muntoni, F....
Neuromuscular Disorders. 33 (2023) - p. S105 , 2023

Link: https://doi.org/10.1016/..

5

P47 ENVISION, a phase 3, randomized trial evaluating the sa..:

Muntoni, F. ; Mercuri, E. ; McDonald, C....
Neuromuscular Disorders. 33 (2023) - p. S70 , 2023

Link: https://doi.org/10.1016/..

6

P36 Givinostat in Duchenne muscular dystrophy: effect on di..:

McDonald, C. ; Servais, L. ; Munell, F....
Neuromuscular Disorders. 33 (2023) - p. S106 , 2023

Link: https://doi.org/10.1016/..

7

P24 Safety and tolerability of Eteplirsen in patients 6–48 ..:

Mercuri, E. ; Seferian, A. ; Deconinck, N....
Neuromuscular Disorders. 33 (2023) - p. S103 , 2023

Link: https://doi.org/10.1016/..

8

P197 Pulmonary function in patients with Duchenne muscular ..:

Tulinius, M. ; Buccella, F. ; Desguerre, I....
Neuromuscular Disorders. 33 (2023) - p. S143 , 2023

Link: https://doi.org/10.1016/..

9

P46 ENVOL, a Phase 2, open-label trial evaluating the safet..:

Mercuri, E. ; Desguerre, I. ; Gangfuss, A....
Neuromuscular Disorders. 33 (2023) - p. S70 , 2023

Link: https://doi.org/10.1016/..

10

P211 Intravenous and intrathecal onasemnogene abeparvovec g..:

Darras, B. ; Mercuri, E. ; Strauss, K....
Neuromuscular Disorders. 33 (2023) - p. S87 , 2023

Link: https://doi.org/10.1016/..

11

P207 Scoliosis progression in spinal muscular atrophy type ..:

Coratti, G. ; Lenkowicz, J. ; Pera, M....
Neuromuscular Disorders. 33 (2023) - p. S86 , 2023

Link: https://doi.org/10.1016/..

12

P117 Congenital recessive TTN myopathy: MRI findings in 6 p..:

Frongia, A. ; Brogna, C. ; Malfatti, E....
Neuromuscular Disorders. 33 (2023) - p. S76 , 2023

Link: https://doi.org/10.1016/..

13

P230 Safety update: Risdiplam clinical trial program for sp..:

Baranello, G. ; Chiriboga, C. ; Servais, L....
Neuromuscular Disorders. 33 (2023) - p. S92-S93 , 2023

Link: https://doi.org/10.1016/..

14

P41 EMBARK, a Phase 3 trial evaluating safety and efficacy ..:

Muntoni, F. ; Mercuri, E. ; Schara-Schmidt, U....
Neuromuscular Disorders. 33 (2023) - p. S68-S69 , 2023

Link: https://doi.org/10.1016/..

15

P129 Givinostat in DMD: results of the Epidys study with pa..:

Vandenborne, K. ; Willcocks, R. ; Walter, G....
Neuromuscular Disorders. 33 (2023) - p. S79-S80 , 2023

Link: https://doi.org/10.1016/..