E-LIB Suche - Ergebnisse für: Auricchio, ALberto

1

CoCas9 is a compact nuclease from the human microbiome for ..:

Pedrazzoli, Eleonora ; Demozzi, Michele ; Visentin, Elisabetta...
Nature Communications. 15 (2024) 1 - p. , 2024

Link: https://doi.org/10.1038/..

2

Safe and effective liver-directed AAV-mediated homology-ind..:

Esposito, Federica ; Dell'Aquila, Fabio ; Rhiel, Manuel...
Cell Reports Medicine. 5 (2024) 7 - p. 101619 , 2024

Link: https://doi.org/10.1016/..

3

Multicentric Longitudinal Prospective Study in a European C..:

Testa, Francesco ; Carreño, Ester ; van den Born, L. Ingeborgh...
Investigative Ophthalmology & Visual Science. 65 (2024) 6 - p. 25 , 2024

Link: https://doi.org/10.1167/..

4

Liver‐directed gene therapy for ornithine aminotransferase ..:

Boffa, Iolanda ; Polishchuk, Elena ; De Stefano, Lucia...
EMBO Molecular Medicine. 15 (2023) 4 - p. , 2023

Link: https://doi.org/10.15252..

5

Efficacy, pharmacokinetics, and safety in the mouse and pri..:

Ferla, Rita ; Dell'Aquila, Fabio ; Doria, Monica...
Molecular Therapy - Methods & Clinical Development. 28 (2023) - p. 396-411 , 2023

Link: https://doi.org/10.1016/..

6

Full-length ATP7B reconstituted through protein trans-splic..:

Padula, Agnese ; Petruzzelli, Raffaella ; Philbert, Sasha A....
Molecular Therapy - Methods & Clinical Development. 26 (2022) - p. 495-504 , 2022

Link: https://doi.org/10.1016/..

7

Liver gene therapy with intein‐mediated F8trans‐splicing co..:

Esposito, Federica ; Lyubenova, Hristiana ; Tornabene, Patrizia...
EMBO Molecular Medicine. 14 (2022) 6 - p. , 2022

Link: https://doi.org/10.15252..

8

miR‐181a/b downregulation: a mutation‐independent therapeut..:

Carrella, Sabrina ; Di Guida, Martina ; Brillante, Simona...
EMBO Molecular Medicine. 14 (2022) 11 - p. , 2022

Link: https://doi.org/10.15252..

9

Therapeutic homology-independent targeted integration in re..:

Tornabene, Patrizia ; Ferla, Rita ; Llado-Santaeularia, Manel...
Nature Communications. 13 (2022) 1 - p. , 2022

Link: https://doi.org/10.1038/..

10

Low incidence of hepatocellular carcinoma in mice and cats ..:

Ferla, Rita ; Alliegro, Marialuisa ; Dell'Anno, Margherita...
Molecular Therapy - Methods & Clinical Development. 20 (2021) - p. 247-257 , 2021

Link: https://doi.org/10.1016/..

11

Allele-specific editing ameliorates dominant retinitis pigm..:

Patrizi, Clarissa ; Llado, Manel ; Benati, Daniela...
The American Journal of Human Genetics. 108 (2021) 2 - p. 295-308 , 2021

Link: https://doi.org/10.1016/..

12

Inclusion of a degron reduces levels of undesired inteins a..:

Tornabene, Patrizia ; Trapani, Ivana ; Centrulo, Miriam...
Molecular Therapy - Methods & Clinical Development. 23 (2021) - p. 448-459 , 2021

Link: https://doi.org/10.1016/..

13

Large gene delivery to the retina with AAV vectors: are we ..:

Trapani, Ivana ; Tornabene, Patrizia ; Auricchio, Alberto
Gene Therapy. 28 (2020) 5 - p. 220-222 , 2020

Link: https://doi.org/10.1038/..

14

The longevity-associated variant of BPIFB4 improves a CXCR4..:

Di Pardo, Alba ; Ciaglia, Elena ; Cattaneo, Monica...
Cell Death & Disease. 11 (2020) 7 - p. , 2020

Link: https://doi.org/10.1038/..

15

Author Correction: A rare genetic variant of BPIFB4 predisp..:

Vecchione, Carmine ; Villa, Francesco ; Carrizzo, Albino...
Scientific Reports. 9 (2019) 1 - p. , 2019

Link: https://doi.org/10.1038/..