Bortolussi, Giulia
95  Ergebnisse:
Personensuche X
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1

CRISPR-Cas9-mediated somatic correction of a one-base delet..:

Bortolussi, Giulia ; Iaconcig, Alessandra ; Canarutto, Giulia...
Molecular Therapy - Methods & Clinical Development.  31 (2023)  - p. 101161 , 2023
 
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Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckli..:

Shi, Xiaoxia ; Aronson, Sem J. ; ten Bloemendaal, Lysbeth...
Molecular Therapy - Methods & Clinical Development.  20 (2021)  - p. 287-297 , 2021
 
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5

Long-term correction of ornithine transcarbamylase deficien..:

De Sabbata, Giulia ; Boisgerault, Florence ; Guarnaccia, Corrado...
Molecular Therapy - Methods & Clinical Development.  20 (2021)  - p. 169-180 , 2021
 
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8

A Quantitative In Vitro Potency Assay for Adeno-Associated ..:

Aronson, Sem J. ; Bakker, Robert S. ; Moenis, Sascha...
Molecular Therapy - Methods & Clinical Development.  18 (2020)  - p. 250-258 , 2020
 
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10

Preclinical Development of an AAV8-hUGT1A1 Vector for the T..:

Collaud, Fanny ; Bortolussi, Giulia ; Guianvarc'h, Laurence...
Molecular Therapy - Methods & Clinical Development.  12 (2019)  - p. 157-174 , 2019
 
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12

Bilirubin-Induced Oxidative Stress Leads to DNA Damage in t..:

Rawat, Vipin ; Bortolussi, Giulia ; Gazzin, Silvia..
Oxidative Medicine and Cellular Longevity.  2018 (2018)  - p. 1-11 , 2018
 
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