E-LIB Suche - Ergebnisse für: Bushby, Katharine

1

Vamorolone trial in Duchenne muscular dystrophy shows dose-..:

Hoffman, Eric P. ; Schwartz, Benjamin D. ; Mengle-Gaw, Laurel J....
Neurology. 93 (2019) 13 - p. , 2019

Link: https://doi.org/10.1212/..

2

Compliance to care guidelines for Duchenne muscular dystrop..:

Landfeldt, Erik ; Lindgren, Peter ; Guglieri, Michela..
Neuromuscular Disorders. 28 (2018) 1 - p. 100 , 2018

Link: https://doi.org/10.1016/..

3

Diagnosis and management of Duchenne muscular dystrophy, pa..:

Birnkrant, David J ; Bushby, Katharine ; Bann, Carla M...
The Lancet Neurology. 17 (2018) 4 - p. 347-361 , 2018

Link: https://doi.org/10.1016/..

4

Psychometric analysis of the pediatric quality of life inve..:

Landfeldt, Erik ; Mayhew, Anna ; Straub, Volker...
Muscle & Nerve. 58 (2018) 3 - p. 367-373 , 2018

Link: https://doi.org/10.1002/..

5

ACT DMD: Effect of Ataluren on Timed Function Tests (TFTs) ..:

Goemans, Nathalie ; Campbell, Craig ; McDonald, Craig...
Neurology. 86 (2016) 16_supplement - p. , 2016

Link: https://doi.org/10.1212/..

6

Results of North Star Ambulatory Assessments (NSAA) in the ..:

Bushby, Katharine ; Kirschner, Jan ; Luo, Xiaohui...
Neurology. 86 (2016) 16_supplement - p. , 2016

Link: https://doi.org/10.1212/..

7

Economic Evaluation in Duchenne Muscular Dystrophy: Model F..:

Landfeldt, Erik ; Alfredsson, Lars ; Straub, Volker...
PharmacoEconomics. 35 (2016) 2 - p. 249-258 , 2016

Link: https://doi.org/10.1007/..

8

Results of North Star Ambulatory Assessments (NSAA) in the ..:

Bushby, Katharine ; Kirschner, Jan ; Luo, Xiaohui...
Neurology. 86 (2016) 16_supplement - p. , 2016

Link: https://doi.org/10.1212/..

9

Ataluren: An Overview of Clinical Trial Results in Nonsense..:

McDonald, Craig ; Bushby, Katharine ; Tulinius, Mar...
Neurology. 86 (2016) 16_supplement - p. , 2016

Link: https://doi.org/10.1212/..

10

Quantifying the burden of caregiving in Duchenne muscular d..:

Landfeldt, Erik ; Lindgren, Peter ; Bell, Christopher F....
Journal of Neurology. 263 (2016) 5 - p. 906-915 , 2016

Link: https://doi.org/10.1007/..

11

Corrigendum to "Development and psychometric analysis of th..:

Landfeldt, Erik ; Mayhew, Anna ; Eagle, Michelle...
Neuromuscular Disorders. 26 (2016) 4-5 - p. 329 , 2016

Link: https://doi.org/10.1016/..

12

Health‐related quality of life in patients with Duchenne mu..:

Landfeldt, Erik ; Lindgren, Peter ; Bell, Christopher F...
Developmental Medicine & Child Neurology. 58 (2015) 5 - p. 508-515 , 2015

Link: https://doi.org/10.1111/..

13

Clinical Management of Dystrophinopathies:

, In: Neuromuscular Disorders of Infancy, Childhood, and Adolescence,

Guglieri, Michela ; Bushby, Katharine - p. 593-619 , 2015

Link: https://doi.org/10.1016/..

14

Development and psychometric analysis of the Duchenne muscu..:

Landfeldt, Erik ; Mayhew, Anna ; Eagle, Michelle...
Neuromuscular Disorders. 25 (2015) 12 - p. 937-944 , 2015

Link: https://doi.org/10.1016/..

15

Compliance to Care Guidelines for Duchenne Muscular Dystrop..:

Landfeldt, Erik ; Lindgren, Peter ; Bell, Christopher F....
Journal of Neuromuscular Diseases. 2 (2015) 1 - p. 63-72 , 2015

Link: https://doi.org/10.3233/..