E-LIB Suche - Ergebnisse für: Chiriboga, Claudia

1

JEWELFISH: 24-month results from an open-label study in non..:

Chiriboga, Claudia A. ; Bruno, Claudio ; Duong, Tina...
Journal of Neurology. , 2024

Link: https://doi.org/10.1007/..

2

Risdiplam in Patients Previously Treated with Other Therapi..:

Chiriboga, Claudia A. ; Bruno, Claudio ; Duong, Tina...
Neurology and Therapy. 12 (2023) 2 - p. 543-557 , 2023

Link: https://doi.org/10.1007/..

3

JEWELFISH: 24-month Safety, Pharmacodynamic and Exploratory..:

Chiriboga, Claudia ; Bruno, Claudio ; Duong, Tina...
Neurology. 100 (2023) 17_supplement_2 - p. , 2023

Link: https://doi.org/10.1212/..

4

Correction to: Risdiplam in Patients Previously Treated wit..:

Chiriboga, Claudia A. ; Bruno, Claudio ; Duong, Tina...
Neurology and Therapy. 12 (2023) 5 - p. 1799-1801 , 2023

Link: https://doi.org/10.1007/..

5

Digital measures of respiratory and upper limb function in ..:

Perumal, Thanneer Malai ; Wolf, Detlef ; Berchtold, Doris...
Neuromuscular Disorders. 33 (2023) 11 - p. 845-855 , 2023

Link: https://doi.org/10.1016/..

6

JEWELFISH: Safety, Pharmacodynamic and Exploratory Efficacy..:

Chiriboga, Claudia A. ; Bruno, Claudio ; Duong, Tina...
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

7

Onasemnogene Abeparvovec in Presymptomatic Spinal Muscular ..:

Strauss, Kevin ; Muntoni, Francesco ; Farrar, Michelle...
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

8

Onasemnogene abeparvovec for presymptomatic infants with tw..:

Strauss, Kevin A. ; Farrar, Michelle A. ; Muntoni, Francesco...
Nature Medicine. 28 (2022) 7 - p. 1381-1389 , 2022

Link: https://doi.org/10.1038/..

9

Onasemnogene abeparvovec for presymptomatic infants with th..:

Strauss, Kevin A. ; Farrar, Michelle A. ; Muntoni, Francesco...
Nature Medicine. 28 (2022) 7 - p. 1390-1397 , 2022

Link: https://doi.org/10.1038/..

10

Pooled Safety Data from the Risdiplam Clinical Trial Develo..:

Darras, Basil T. ; Chiriboga, Claudia A. ; Servais, Laurent...
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

11

Newborn Screening for Spinal Muscular Atrophy in New York S..:

Lee, Bo Hoon ; Deng, Stella ; Chiriboga, Claudia A....
Neurology. 99 (2022) 14 - p. , 2022

Link: https://doi.org/10.1212/..

12

Pharmacotherapy for Spinal Muscular Atrophy in Babies and C..:

Chiriboga, Claudia A.
Pediatric Drugs. 24 (2022) 6 - p. 585-602 , 2022

Link: https://doi.org/10.1007/..

13

Onasemnogene Abeparvovec for Presymptomatic Infants with Sp..:

Strauss, Kevin ; Muntoni, Francesco ; Farrar, Michelle...
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

14

Pooled Safety Data from the Risdiplam Clinical Trial Develo..:

Servais, Laurent ; Baranello, Giovanni ; Bertini, Enrico...
Neurology. 96 (2021) 15_supplement - p. , 2021

Link: https://doi.org/10.1212/..

15

Improving Care and Empowering Adults Living with SMA: A Cal..:

Walter, Maggie C. ; Chiriboga, Claudia ; Duong, Tina...
Journal of Neuromuscular Diseases. 8 (2021) 4 - p. 543-551 , 2021

Link: https://doi.org/10.3233/..