E-LIB Suche - Ergebnisse für: Deborah A Zygmunt

1

Dual FKRP/FST gene therapy normalizes ambulation, increases..:

Lam, Patricia ; Zygmunt, Deborah A. ; Ashbrook, Anna...
Molecular Therapy. , 2024

Link: https://doi.org/10.1016/..

2

Liver-directed AAV gene therapy corrects disease symptoms i..:

Lam, Patricia ; Zygmunt, Deborah ; Ashbrook, Anna...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107930 , 2024

Link: https://doi.org/10.1016/..

3

Development of Assays to Measure GNE Gene Potency and Gene ..:

Zygmunt, Deborah A. ; Lam, Patricia ; Ashbrook, Anna...
Journal of Neuromuscular Diseases. 10 (2023) 5 - p. 797-812 , 2023

Link: https://doi.org/10.3233/..

4

Therapeutic efficacy of rscAAVrh74.miniCMV.LIPA gene therap..:

Lam, Patricia ; Ashbrook, Anna ; Zygmunt, Deborah A....
Molecular Therapy - Methods & Clinical Development. 26 (2022) - p. 413-426 , 2022

Link: https://doi.org/10.1016/..

5

A first-in-human phase I/IIa gene transfer clinical trial f..:

Flanigan, Kevin M. ; Vetter, Tatyana A. ; Simmons, Tabatha R....
Molecular Therapy - Methods & Clinical Development. 27 (2022) - p. 47-60 , 2022

Link: https://doi.org/10.1016/..

6

Short-term treatment of golden retriever muscular dystrophy..:

Martin, Paul T. ; Zygmunt, Deborah A. ; Ashbrook, Anna...
PLOS ONE. 16 (2021) 3 - p. e0248721 , 2021

Link: https://doi.org/10.1371/..

7

rAAVrh74.MCK.GALGT2 Protects against Loss of Hemodynamic Fu..:

Xu, Rui ; Jia, Ying ; Zygmunt, Deborah A..
Molecular Therapy. 27 (2019) 3 - p. 636-649 , 2019

Link: https://doi.org/10.1016/..

8

rAAVrh74.MCK.GALGT2 Demonstrates Safety and Widespread Musc..:

Zygmunt, Deborah A. ; Xu, Rui ; Jia, Ying...
Molecular Therapy - Methods & Clinical Development. 15 (2019) - p. 305-319 , 2019

Link: https://doi.org/10.1016/..

9

Expansion of B4GALT7 linkeropathy phenotype to include peri..:

Mihalic Mosher, Theresa ; Zygmunt, Deborah A. ; Koboldt, Daniel C....
European Journal of Human Genetics. 27 (2019) 10 - p. 1569-1577 , 2019

Link: https://doi.org/10.1038/..

10

An Isolated Limb Infusion Method Allows for Broad Distribut..:

Xu, Rui ; Jia, Ying ; Zygmunt, Deborah A....
Molecular Therapy - Methods & Clinical Development. 10 (2018) - p. 89-104 , 2018

Link: https://doi.org/10.1016/..

11

Active and passive immunization strategies based on the SDP..:

Camboni, Marybeth ; Wang, Chiou-Miin ; Miranda, Carlos...
Neurobiology of Disease. 62 (2014) - p. 31-43 , 2014

Link: https://doi.org/10.1016/..

12

O2–06–05: Active and passive immunization strategies based ..:

Martin, Paul ; Wang, Chiou‐Miin ; Camboni, Marybeth...
Alzheimer's & Dementia. 9 (2013) 4S_Part_8 - p. , 2013

Link: https://doi.org/10.1016/..

13

Quantitation of viral DNA in renal allograft tissue from pa..:

Randhawa, Parmjeet S. ; Vats, Abhay ; Zygmunt, Deborah...
Transplantation. 74 (2002) 4 - p. 485-488 , 2002

Link: https://doi.org/10.1097/..

14

Toxoplasmosis A preventable infection of increasing importa..:

Zygmunt, Deborah J.
Infectious Diseases Newsletter. 9 (1990) 7 - p. 49-52 , 1990

Link: https://doi.org/10.1016/..

15

Cryptosporidium-induced diarrhea from the exotic to the com..:

Zygmunt, Deborah J.
Infectious Diseases Newsletter. 9 (1990) 4 - p. 28-29 , 1990

Link: https://doi.org/10.1016/..