Bush, Jessica A ;
Meyer, Samantha M ;
Fuerst, Rita...
Bush , J A , Meyer , S M , Fuerst , R , Tong , Y , Li , Y , Benhamou , R I , Aikawa , H , Zanon , P R A , Gibaut , Q M R , Angelbello , A J , Gendron , T F , Zhang , Y J , Petrucelli , L , Heick Jensen , T , Childs-Disney , J L & Disney , M D 2022 , ' A blood-brain penetrant RNA-targeted small molecule triggers elimination of r(G 4 C 2 ) exp in c9ALS/FTD via the nuclear RNA exosome ' , Proceedings of the National Academy of Sciences , vol. 119 , no. 48 , e2210532119 . https://doi.org/10.1073/pnas.2210532119.
,
2022
