E-LIB Suche - Ergebnisse für: Gray-Edwards, Heather L.

1

Adeno-associated viral gene therapy for sialidosis using sm..:

Gallagher, Jillian ; Gallant, Judith ; Xu, Ping...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107834 , 2024

Link: https://doi.org/10.1016/..

2

A pentasaccharide for monitoring pharmacodynamic response t..:

Kell, Pamela ; Sidhu, Rohini ; Qian, Mingxing...
eBioMedicine. 92 (2023) - p. 104627 , 2023

Link: https://doi.org/10.1016/..

3

From mouse to sheep: Generating a sheep model and developin..:

Gallagher, Jillian ; Gallant, Judith ; Xu, Ping...
Molecular Genetics and Metabolism. 138 (2023) 2 - p. 107109 , 2023

Link: https://doi.org/10.1016/..

4

Adeno-associated virus-mediated gene therapy in a patient w..:

Corti, Manuela ; Byrne, Barry J. ; Gessler, Dominic J....
Molecular Therapy - Methods & Clinical Development. 30 (2023) - p. 303-314 , 2023

Link: https://doi.org/10.1016/..

5

BSLD-01 DYNAMIC CONTROL OF CSF FOR PERSONALIZED CNS DRUG DE..:

Kumthekar, Priya ; Benatti, Hector Ribeiro ; Taghian, Toloo...
Neuro-Oncology Advances. 5 (2023) Supplement_3 - p. iii5-iii6 , 2023

Link: https://doi.org/10.1093/..

6

Levels of Synaptic Proteins in Brain and Neurofilament Ligh..:

Sapp, Ellen ; Boudi, Adel ; Reid, Suzanne J....
Journal of Huntington's Disease. 12 (2023) 3 - p. 201-213 , 2023

Link: https://doi.org/10.3233/..

7

Awake intracerebroventricular delivery and safety assessmen..:

Benatti, Hector Ribeiro ; Prestigiacomo, Rachel D. ; Taghian, Toloo...
Molecular Therapy - Methods & Clinical Development. 31 (2023) - p. 101122 , 2023

Link: https://doi.org/10.1016/..

8

Gene-based therapeutics for rare genetic neurodevelopmental..:

Davidson, Beverly L. ; Gao, Guangping ; Berry-Kravis, Elizabeth...
Molecular Therapy. 30 (2022) 7 - p. 2416-2428 , 2022

Link: https://doi.org/10.1016/..

9

DDEL-01. ANIMAL STUDIES WITH A NEW CNS DRUG DELIVERY DEVICE..:

Kumthekar, Priya ; Benatti, Hector ; Taghian, Toloo...
Neuro-Oncology. 24 (2022) Supplement_7 - p. vii94-vii94 , 2022

Link: https://doi.org/10.1093/..

10

AAV gene therapy for Tay-Sachs disease:

Flotte, Terence R. ; Cataltepe, Oguz ; Puri, Ajit...
Nature Medicine. 28 (2022) 2 - p. 251-259 , 2022

Link: https://doi.org/10.1038/..

11

Brain Alterations in Aged OVT73 Sheep Model of Huntington's..:

Taghian, Toloo ; Gallagher, Jillian ; Batcho, Erin...
Journal of Huntington's Disease. 11 (2022) 4 - p. 391-406 , 2022

Link: https://doi.org/10.3233/..

12

Sialidosis: From gene editing to gene therapy:

Gallagher, Jillian ; Gallant, Judith ; Xu, Ping...
Molecular Genetics and Metabolism. 135 (2022) 2 - p. S45 , 2022

Link: https://doi.org/10.1016/..

13

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy - Methods & Clinical Development. 27 (2022) - p. 281-292 , 2022

Link: https://doi.org/10.1016/..

14

A comprehensive study of a 29-capsid AAV library in a non-h..:

Kondratov, Oleksandr ; Kondratova, Liudmyla ; Mandel, Ronald J....
Molecular Therapy. 29 (2021) 9 - p. 2806-2820 , 2021

Link: https://doi.org/10.1016/..

15

Intravenous delivery of adeno-associated viral gene therapy..:

Gross, Amanda L ; Gray-Edwards, Heather L ; Bebout, Cassie N...
Brain. 145 (2021) 2 - p. 655-669 , 2021

Link: https://doi.org/10.1093/..