E-LIB Suche - Ergebnisse für: Hocquemiller, Michaël

1

Design of a stable human acid‐β‐glucosidase: towards improv..:

Pokorna, Sarka ; Khersonsky, Olga ; Lipsh‐Sokolik, Rosalie...
The FEBS Journal. 290 (2023) 13 - p. 3383-3399 , 2023

2

Focal lesions following intracerebral gene therapy for muco..:

Bugiani, Marianna ; Abbink, Truus E. M. ; Edridge, Arthur W. D....
Annals of Clinical and Translational Neurology. 10 (2023) 6 - p. 904-917 , 2023

Link: https://doi.org/10.1002/..

3

AAVance gene therapy study in children with mucopolysacchar..:

Laufer, Ralph ; Drevot, Philippe ; Hocquemiller, Michaël...
Molecular Genetics and Metabolism. 135 (2022) 2 - p. S71-S72 , 2022

Link: https://doi.org/10.1016/..

4

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy - Methods & Clinical Development. 27 (2022) - p. 281-292 , 2022

Link: https://doi.org/10.1016/..

5

AAV‐delivered diacylglycerol kinase DGKk achieves long‐term..:

Habbas, Karima ; Cakil, Oktay ; Zámbó, Boglárka...
EMBO Molecular Medicine. 14 (2022) 5 - p. , 2022

Link: https://doi.org/10.15252..

6

AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice ..:

Hocquemiller, Michaël ; Hemsley, Kim M. ; Douglass, Meghan L....
Molecular Therapy - Methods & Clinical Development. 17 (2020) - p. 174-187 , 2020

Link: https://doi.org/10.1016/..

7

AAV gene therapy LYS-SAF302 demonstrates widespread sulfami..:

Laufer, Ralph ; Hocquemiller, Michael ; Hemsley, Kim
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S91-S92 , 2019

Link: https://doi.org/10.1016/..

8

AAVrh10-SGSH intracerebral gene therapy corrects the defect..:

Parker, Samantha ; Hocquemiller, Michaël ; le Meur, Alice
Molecular Genetics and Metabolism. 114 (2015) 2 - p. S90 , 2015

Link: https://doi.org/10.1016/..

9

58. Abnormal vacuoles distinct from lysosomes in a mouse mo..:

Heard, Jean-Michel ; Vitry, Sandrine ; Bruyère, Julie...
Molecular Genetics and Metabolism. 99 (2010) 2 - p. S20 , 2010

Link: https://doi.org/10.1016/..

10

Enhanced degradation of synaptophysin by the proteasome in ..:

Vitry, Sandrine ; Ausseil, Jérôme ; Hocquemiller, Michael...
Molecular and Cellular Neuroscience. 41 (2009) 1 - p. 8-18 , 2009

Link: https://doi.org/10.1016/..

11

GAP43 overexpression and enhanced neurite outgrowth in muco..:

Hocquemiller, Michaël ; Vitry, Sandrine ; Bigou, Stéphanie...
Journal of Neuroscience Research. 88 (2009) 1 - p. 202-213 , 2009

Link: https://doi.org/10.1002/..

12

Directed Evolution of Motor Neurons from Genetically Engine..:

Bohl, Delphine ; Liu, Song ; Blanchard, Stéphane...
Stem Cells. 26 (2008) 10 - p. 2564-2575 , 2008

Link: https://doi.org/10.1634/..

13

Forced expression of the motor neuron determinant HB9 in ne..:

Bréjot, Thomas ; Blanchard, Stéphane ; Hocquemiller, Michaël...
Experimental Neurology. 198 (2006) 1 - p. 167-182 , 2006

Link: https://doi.org/10.1016/..

14

α-l-Iduronidase transport in neurites:

Chen, Fengtian ; Vitry, Sandrine ; Hocquemiller, Michaël...
Molecular Genetics and Metabolism. 87 (2006) 4 - p. 349-358 , 2006

Link: https://doi.org/10.1016/..

15

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy – Methods & Clinical Development. , 2023

Link: https://doi.org/10.1016/..