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X
Iannaccone, Susan T.
259  Ergebnisse:
Personensuche X
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1

Adherence and Persistence Among Risdiplam-Treated Individua..:

Pineda, Elmor D. ; To, Tu My ; Dickendesher, Travis L...
Advances in Therapy.  41 (2024)  6 - p. 2446-2459 , 2024
Link: https://doi.org/10.1007/..
 
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2

Access to novel therapies for Duchenne muscular dystrophy—I..:

Veerapandiyan, Aravindhan ; Connolly, Anne M. ; Mathews, Katherine D....
Annals of the Child Neurology Society.  , 2024
Link: https://doi.org/10.1002/..
 
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3

Observing the Clinical Course of Duchenne Muscular Dystroph..:

Qian, Christina ; Klimchak, Alexa C. ; Szabo, Shelagh M....
Advances in Therapy.  41 (2024)  6 - p. 2519-2530 , 2024
Link: https://doi.org/10.1007/..
 
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4

Immune-mediated myositis following gene therapy for Duchenn..:

Iannaccone, Susan T. ; Cai, Chunyu ; Rhem, Brittney...
Journal of Neurology.  271 (2024)  8 - p. 5659-5664 , 2024
Link: https://doi.org/10.1007/..
 
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5

Patterns of developmental regression and associated clinica..:

Kalvakuntla, Sanjana ; Lee, MinJae ; Chung, Wendy K....
Frontiers in Neuroscience.  17 (2023)  - p. , 2023
Link: https://doi.org/10.3389/..
 
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6

Ectopic PLAG1 induces muscular dystrophy in the mouse:

Aguayo, Juan Shugert ; Shelton, John M. ; Tan, Wei...
Biochemical and Biophysical Research Communications.  665 (2023)  - p. 159-168 , 2023
Link: https://doi.org/10.1016/..
 
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7

Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambula..:

Finkel, Richard S. ; Darras, Basil T. ; Mendell, Jerry R....
Journal of Neuromuscular Diseases.  10 (2023)  3 - p. 389-404 , 2023
Link: https://doi.org/10.3233/..
 
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8

Estimating health state utilities in Duchenne muscular dyst..:

Audhya, Ivana F. ; Szabo, Shelagh M. ; Bever, Andrea...
Journal of Patient-Reported Outcomes.  7 (2023)  1 - p. , 2023
Link: https://doi.org/10.1186/..
 
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9

Onasemnogene abeparvovec for presymptomatic infants with tw..:

Strauss, Kevin A. ; Farrar, Michelle A. ; Muntoni, Francesco...
Nature Medicine.  28 (2022)  7 - p. 1381-1389 , 2022
Link: https://doi.org/10.1038/..
 
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10

Restoration of Nusinersen Levels Following Treatment Interr..:

MacCannell, Drew ; Berger, Zdenek ; Kirschner, Janbernd...
CNS Drugs.  36 (2022)  2 - p. 181-190 , 2022
Link: https://doi.org/10.1007/..
 
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11

Biallelic variants in TAMM41 are associated with low muscle..:

Thompson, Kyle ; Bianchi, Lucas ; Rastelli, Francesca...
Human Genetics and Genomics Advances.  3 (2022)  2 - p. 100097 , 2022
Link: https://doi.org/10.1016/..
 
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12

Onasemnogene abeparvovec for presymptomatic infants with th..:

Strauss, Kevin A. ; Farrar, Michelle A. ; Muntoni, Francesco...
Nature Medicine.  28 (2022)  7 - p. 1390-1397 , 2022
Link: https://doi.org/10.1038/..
 
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13

Adherence and Persistence to Nusinersen for Spinal Muscular..:

Fox, David ; To, Tu My ; Seetasith, Arpamas..
Advances in Therapy.  40 (2022)  3 - p. 903-919 , 2022
Link: https://doi.org/10.1007/..
 
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14

Social Media and Clinical Trials in Pediatric Disease: Musi..:

Nelson, Leslie ; Iannaccone, Susan T.
Frontiers in Genetics.  12 (2021)  - p. , 2021
Link: https://doi.org/10.3389/..
 
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15

Johann Hoffmann:

, In: Child Neurology,
Iannaccone, Susan T. ; Caneris, Onasis - p. 117-119 , 2021
Link: https://doi.org/10.1016/..
 
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