E-LIB Suche - Ergebnisse für: Laufer, Ralph

1

Design of a stable human acid‐β‐glucosidase: towards improv..:

Pokorna, Sarka ; Khersonsky, Olga ; Lipsh‐Sokolik, Rosalie...
The FEBS Journal. 290 (2023) 13 - p. 3383-3399 , 2023

2

Focal lesions following intracerebral gene therapy for muco..:

Bugiani, Marianna ; Abbink, Truus E. M. ; Edridge, Arthur W. D....
Annals of Clinical and Translational Neurology. 10 (2023) 6 - p. 904-917 , 2023

Link: https://doi.org/10.1002/..

3

AAVance gene therapy study in children with mucopolysacchar..:

Laufer, Ralph ; Drevot, Philippe ; Hocquemiller, Michaël...
Molecular Genetics and Metabolism. 135 (2022) 2 - p. S71-S72 , 2022

Link: https://doi.org/10.1016/..

4

AAV‐delivered diacylglycerol kinase DGKk achieves long‐term..:

Habbas, Karima ; Cakil, Oktay ; Zámbó, Boglárka...
EMBO Molecular Medicine. 14 (2022) 5 - p. , 2022

Link: https://doi.org/10.15252..

5

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy - Methods & Clinical Development. 27 (2022) - p. 281-292 , 2022

Link: https://doi.org/10.1016/..

6

Efficacy of PEGylated ciliary neurotrophic factor superagon..:

Battista, Maria Rosaria ; Grigoletto, Antonella ; Tedeschini, Tommaso...
PLOS ONE. 17 (2022) 3 - p. e0265749 , 2022

Link: https://doi.org/10.1371/..

7

AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice ..:

Hocquemiller, Michaël ; Hemsley, Kim M. ; Douglass, Meghan L....
Molecular Therapy - Methods & Clinical Development. 17 (2020) - p. 174-187 , 2020

Link: https://doi.org/10.1016/..

8

AAV gene therapy LYS-SAF302 demonstrates widespread sulfami..:

Laufer, Ralph ; Hocquemiller, Michael ; Hemsley, Kim
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S91-S92 , 2019

Link: https://doi.org/10.1016/..

9

Pridopidine Treatment Recovers Gait Abnormalities and Rescu..:

Geva, Michal ; Dreymann, Jennifer ; Barash, Steve...
Neurology. 90 (2018) 15_supplement - p. , 2018

Link: https://doi.org/10.1212/..

10

Pridopidine, a clinic‐ready compound, reduces 3,4‐dihydroxy..:

Johnston, Tom H. ; Geva, Michal ; Steiner, Lilach...
Movement Disorders. 34 (2018) 5 - p. 708-716 , 2018

Link: https://doi.org/10.1002/..

11

Physicochemical and Biological Characterization of both Cop..:

Timan, Bracha ; Komlosh, Arthur ; Beriozkin, Olga...
Neurology. 90 (2018) 15_supplement - p. , 2018

Link: https://doi.org/10.1212/..

12

Laquinimod targets the aryl hydrocarbon receptor (AhR) path..:

Birnberg, Tal ; Kaye, Joel ; Fowler, Kevin...
Neurology. 88 (2017) 16_supplement - p. , 2017

Link: https://doi.org/10.1212/..

13

Pharmacogenomics strategies to optimize treatments for mult..:

Grossman, Iris ; Knappertz, Volker ; Laifenfeld, Daphna...
Progress in Neurobiology. 152 (2017) - p. 114-130 , 2017

Link: https://doi.org/10.1016/..

14

Laquinimod modulates central nervous system inflammation vi..:

Kaye, Joel ; Laufer, Ralph ; Kenison, Jessica..
Neurology. 88 (2017) 16_supplement - p. , 2017

Link: https://doi.org/10.1212/..

15

Laquinimod arrests experimental autoimmune encephalomyeliti..:

Kaye, Joel ; Piryatinsky, Victor ; Birnberg, Tal...
Proceedings of the National Academy of Sciences of the United States of America. 113 (2016) 41 - p. E6145-E6152 , 2016

Link: https://www.jstor.org/st..