E-LIB Suche - Ergebnisse für: Lehman, Kelly

1

Gene therapy with bidridistrogene xeboparvovec for limb-gir..:

Mendell, Jerry R. ; Pozsgai, Eric R. ; Lewis, Sarah...
Nature Medicine. 30 (2024) 1 - p. 199-206 , 2024

2

Expression of SRP-9001 dystrophin and stabilization of moto..:

Mendell, Jerry R. ; Shieh, Perry B. ; McDonald, Craig M....
Frontiers in Cell and Developmental Biology. 11 (2023) - p. , 2023

Link: https://doi.org/10.3389/..

3

Long‐term safety and functional outcomes of delandistrogene..:

Mendell, Jerry R. ; Sahenk, Zarife ; Lehman, Kelly J....
Muscle & Nerve. 69 (2023) 1 - p. 93-98 , 2023

Link: https://doi.org/10.1002/..

4

P314: Long-term safety and sustained functional benefit in ..:

O'Rourke, Erin ; Mendell, Jerry R. ; Sahenk, Zarife...
Genetics in Medicine Open. 1 (2023) 1 - p. 100342 , 2023

Link: https://doi.org/10.1016/..

5

Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Pat..:

Zaidman, Craig M. ; Proud, Crystal M. ; McDonald, Craig M....
Annals of Neurology. 94 (2023) 5 - p. 955-968 , 2023

Link: https://doi.org/10.1002/..

6

Long-term Safety and Efficacy in Patients with DMD 4 Years ..:

Mendell, Jerry ; Sahenk, Zarife ; Lehman, Kelly...
Neurology. 100 (2023) 17_supplement_2 - p. , 2023

Link: https://doi.org/10.1212/..

7

A Phase 2 Clinical Trial Evaluating the Safety and Efficacy..:

Mendell, Jerry ; Shieh, Perry ; Sahenk, Zarife...
Neurology. 100 (2023) 17_supplement_2 - p. , 2023

Link: https://doi.org/10.1212/..

8

Safety, β-Sarcoglycan Expression, and Functional Outcomes F..:

Rodino-Klapac, Louise R. ; Pozsgai, Eric R. ; Lewis, Sarah...
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

9

eP212: Safety, β-Sarcoglycan expression, and functional out..:

O'Rourke, Erin ; Rodino-Klapac, Louise ; Pozsgai, Eric...
Genetics in Medicine. 24 (2022) 3 - p. S132-S133 , 2022

Link: https://doi.org/10.1016/..

10

Phase 1/2a Trial of SRP-9001 in Patients with Duchenne Musc..:

Mendell, Jerry R. ; Sahenk, Zarife ; Lehman, Kelly J....
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

11

A Phase 2 Clinical Trial Evaluating the Safety and Efficacy..:

Mendell, Jerry R. ; Shieh, Perry B. ; Sahenk, Zarife...
Neurology. 98 (2022) 18_supplement - p. , 2022

Link: https://doi.org/10.1212/..

12

eP201: A phase 2 clinical trial evaluating the safety and e..:

O'Rourke, Erin ; Mendell, Jerry ; Shieh, Perry...
Genetics in Medicine. 24 (2022) 3 - p. S124 , 2022

Link: https://doi.org/10.1016/..

13

Testing preexisting antibodies prior to AAV gene transfer t..:

Mendell, Jerry R. ; Connolly, Anne M. ; Lehman, Kelly J....
Molecular Therapy - Methods & Clinical Development. 25 (2022) - p. 74-83 , 2022

Link: https://doi.org/10.1016/..

14

Safety, β-sarcoglycan Expression and Functional Outcomes fr..:

Rodino-Klapac, Louise ; Pozsgai, Eric ; Lewis, Sarah...
Neurology. 96 (2021) 15_supplement - p. , 2021

Link: https://doi.org/10.1212/..

15

Unmet Needs and Evolving Treatment for Limb Girdle Muscular..:

Pozsgai, Eric ; Griffin, Danielle ; Potter, Rachael...
Neurodegenerative Disease Management. 11 (2021) 5 - p. 411-429 , 2021

Link: https://doi.org/10.2217/..