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Malkus, Betsy C.
46  Ergebnisse:
Personensuche X
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1

Performance measures and patient/caregiver-reported assessm..:

Malkus, Betsy C. ; Cohen, Jeanne M. ; Grant, Christina L....
Molecular Genetics and Metabolism.  141 (2024)  2 - p. 107949 , 2024
Link: https://doi.org/10.1016/..
 
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2

Long-term efficacy and safety of vestronidase alfa enzyme r..:

Lau, Heather ; Viskochil, David ; Tanpaiboon, Pranoot...
Molecular Genetics and Metabolism.  129 (2020)  2 - p. S95 , 2020
Link: https://doi.org/10.1016/..
 
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3

Pentoxifylline as a rescue treatment for DMD: A randomized ..:

Escolar, D.M ; Zimmerman, A ; Bertorini, T...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC3306159.  , 2012
Link: http://www.ncbi.nlm.nih...
 
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4

Characterization of Strength and Function in Ambulatory Adu..:

Argov, Zohar ; Bronstein, Faye ; Esposito, Alicia...
Journal of Clinical Neuromuscular Disease.  19 (2017)  1 - p. 19-26 , 2017
Link: https://doi.org/10.1097/..
 
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5

Clinical trial readiness in non-ambulatory boys and men wit..:

Connolly, Anne M. ; Florence, Julaine M. ; Zaidman, Craig M....
Muscle & Nerve.  54 (2016)  4 - p. 681-689 , 2016
Link: https://doi.org/10.1002/..
 
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6

Outcome reliability in non‐Ambulatory Boys/Men with duchenn..:

Connolly, Anne M. ; Malkus, Elizabeth C. ; Mendell, Jerry R....
Muscle & Nerve.  51 (2015)  4 - p. 522-532 , 2015
Link: https://doi.org/10.1002/..
 
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7

Muscle ultrasound quantifies disease progression over time ..:

Zaidman, Craig M. ; Malkus, Elizabeth C. ; Connolly, Anne M.
Muscle & Nerve.  52 (2015)  3 - p. 334-338 , 2015
Link: https://doi.org/10.1002/..
 
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8

One Year Outcome of Boys With Duchenne Muscular Dystrophy U..:

Connolly, Anne M. ; Florence, Julaine M. ; Cradock, Mary M....
Pediatric Neurology.  50 (2014)  6 - p. 557-563 , 2014
Link: https://doi.org/10.1016/..
 
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9

G.P.167:

Connolly, A.M. ; Malkus, E.C. ; Schierbecker, J.R....
Neuromuscular Disorders.  24 (2014)  9-10 - p. 855-856 , 2014
Link: https://doi.org/10.1016/..
 
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10

P.7.16 One year outcome assessment of young boys with DMD u..:

Connolly, A.M. ; Florence, J.M. ; Cradock, M.M....
Neuromuscular Disorders.  23 (2013)  9-10 - p. 778 , 2013
Link: https://doi.org/10.1016/..
 
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11

Motor and cognitive assessment of infants and young boys wi..:

Connolly, Anne M. ; Florence, Julaine M. ; Cradock, Mary M....
Neuromuscular Disorders.  23 (2013)  7 - p. 529-539 , 2013
Link: https://doi.org/10.1016/..
 
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12

Qualitative and quantitative skeletal muscle ultrasound in ..:

Zaidman, Craig M. ; Malkus, Elizabeth C. ; Siener, Catherine...
Muscle & Nerve.  44 (2011)  3 - p. 418-423 , 2011
Link: https://doi.org/10.1002/..
 
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13

Quantitative ultrasound using backscatter analysis in Duche..:

Zaidman, Craig M. ; Connolly, Anne M. ; Malkus, Elizabeth C...
Neuromuscular Disorders.  20 (2010)  12 - p. 805-809 , 2010
Link: https://doi.org/10.1016/..
 
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14

Trial interviews to explore glycogen storage disease type I..:

Turner-Bowker, Diane ; Malkus, Betsy ; Egan, Shayna...
Molecular Genetics and Metabolism.  141 (2024)  4 - p. 108269 , 2024
Link: https://doi.org/10.1016/..
 
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15

Early clinical response and continued safety with vestronid..:

Burton, Barbara ; Giugliani, Roberto ; Gonzalez-Meneses, Antonio...
Molecular Genetics and Metabolism.  141 (2024)  4 - p. 108212 , 2024
Link: https://doi.org/10.1016/..
 
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