E-LIB Suche - Ergebnisse für: Marais, Thibaut

1

Muscle regeneration affects Adeno Associated Virus 1 mediat..:

Mollard, Amédée ; Peccate, Cécile ; Forand, Anne...
Scientific Reports. 12 (2022) 1 - p. , 2022

Link: https://doi.org/10.1038/..

2

Promoterless Gene Targeting Approach Combined to CRISPR/Cas..:

Lisjak, Michela ; De Caneva, Alessia ; Marais, Thibaut...
Frontiers in Genome Editing. 4 (2022) - p. , 2022

Link: https://doi.org/10.3389/..

3

The non-muscle ADF/cofilin-1 controls sarcomeric actin fila..:

Vignier, Nicolas ; Chatzifrangkeskou, Maria ; Pinton, Luca...
Cell Reports. 36 (2021) 8 - p. 109601 , 2021

Link: https://doi.org/10.1016/..

4

Systemic Treatment of Fabry Disease Using a Novel AAV9 Vect..:

Biferi, Maria Grazia ; Cohen-Tannoudji, Mathilde ; García-Silva, Andrea...
Molecular Therapy - Methods & Clinical Development. 20 (2021) - p. 1-17 , 2021

Link: https://doi.org/10.1016/..

5

AAV9-Mediated Expression of SMN Restricted to Neurons Does ..:

Besse, Aurore ; Astord, Stephanie ; Marais, Thibaut...
Molecular Therapy. 28 (2020) 8 - p. 1887-1901 , 2020

Link: https://doi.org/10.1016/..

6

Activation of sarcolipin expression and altered calcium cyc..:

Morales Rodriguez, Blanca ; Domínguez-Rodríguez, Alejandro ; Benitah, Jean-Pierre...
Biochemistry and Biophysics Reports. 22 (2020) - p. 100767 , 2020

Link: https://doi.org/10.1016/..

7

Cofilin-1 phosphorylation catalyzed by ERK1/2 alters cardia..:

Chatzifrangkeskou, Maria ; Yadin, David ; Marais, Thibaut...
Human Molecular Genetics. 27 (2018) 17 - p. 3060-3078 , 2018

Link: https://doi.org/10.1093/..

8

Intravenous administration of scAAV9-Hexb normalizes lifesp..:

Niemir, Natalia ; Rouvière, Laura ; Besse, Aurore...
Human Molecular Genetics. 27 (2018) 6 - p. 954-968 , 2018

Link: https://doi.org/10.1093/..

9

A New AAV10-U7-Mediated Gene Therapy Prolongs Survival and ..:

Biferi, Maria Grazia ; Cohen-Tannoudji, Mathilde ; Cappelletto, Ambra...
Molecular Therapy. 25 (2017) 9 - p. 2038-2052 , 2017

Link: https://doi.org/10.1016/..

10

Efficacy and biodistribution analysis of intracerebroventri..:

Armbruster, Nicole ; Lattanzi, Annalisa ; Jeavons, Matthieu...
Molecular Therapy - Methods & Clinical Development. 3 (2016) - p. 16060 , 2016

Link: https://doi.org/10.1038/..

11

Lentiviral vector-mediated overexpression of mutant ataxin-..:

Alves, Sandro ; Marais, Thibaut ; Biferi, Maria-Grazia...
Molecular Neurodegeneration. 11 (2016) 1 - p. , 2016

Link: https://doi.org/10.1186/..

12

Systemic AAVrh10 provides higher transgene expression than ..:

Tanguy, Yannick ; Biferi, Maria G. ; Besse, Aurore...
Frontiers in Molecular Neuroscience. 8 (2015) - p. , 2015

Link: https://doi.org/10.3389/..

13

The autophagy/lysosome pathway is impaired in SCA7 patients..:

Alves, Sandro ; Cormier-Dequaire, Florence ; Marinello, Martina...
Acta Neuropathologica. 128 (2014) 5 - p. 705-722 , 2014

Link: https://doi.org/10.1007/..

14

Intramuscular scAAV9-SMN Injection Mediates Widespread Gene..:

Benkhelifa-Ziyyat, Sofia ; Besse, Aurore ; Roda, Marianne...
Molecular Therapy. 21 (2013) 2 - p. 282-290 , 2013

Link: https://doi.org/10.1038/..

15

Intravenous scAAV9 delivery of a codon-optimized SMN1 seque..:

Dominguez, Elisa ; Marais, Thibaut ; Chatauret, Nicolas...
Human Molecular Genetics. 20 (2010) 4 - p. 681-693 , 2010

Link: https://doi.org/10.1093/..