E-LIB Suche - Ergebnisse für: Maule, Giulia

1

CoCas9 is a compact nuclease from the human microbiome for ..:

Pedrazzoli, Eleonora ; Demozzi, Michele ; Visentin, Elisabetta...
Nature Communications. 15 (2024) 1 - p. , 2024

Link: https://doi.org/10.1038/..

2

Prime editing functionally corrects cystic fibrosis-causing..:

Bulcaen, Mattijs ; Kortleven, Phéline ; Liu, Ronald B....
Cell Reports Medicine. 5 (2024) 5 - p. 101544 , 2024

Link: https://doi.org/10.1016/..

3

Functional restoration of a CFTR splicing mutation through ..:

Amistadi, Simone ; Maule, Giulia ; Ciciani, Matteo...
Molecular Therapy. 31 (2023) 6 - p. 1647-1660 , 2023

Link: https://doi.org/10.1016/..

4

Base-editing-mediated dissection of a γ-globin cis-regulato..:

Antoniou, Panagiotis ; Hardouin, Giulia ; Martinucci, Pierre...
Nature Communications. 13 (2022) 1 - p. , 2022

Link: https://doi.org/10.1038/..

5

Combination of lentiviral and genome editing technologies f..:

Ramadier, Sophie ; Chalumeau, Anne ; Felix, Tristan...
Molecular Therapy. 30 (2022) 1 - p. 145-163 , 2022

Link: https://doi.org/10.1016/..

6

Generation of corrected hiPSC clones from a Cornelia de Lan..:

Umbach, Alessandro ; Maule, Giulia ; Kheir, Eyemen...
Stem Cell Research & Therapy. 13 (2022) 1 - p. , 2022

Link: https://doi.org/10.1186/..

7

Correction of β-thalassemia by CRISPR/Cas9 editing of the α..:

Pavani, Giulia ; Fabiano, Anna ; Laurent, Marine...
Blood Advances. 5 (2021) 5 - p. 1137-1153 , 2021

Link: https://doi.org/10.1182/..

8

Author Correction: Allele specific repair of splicing mutat..:

Maule, Giulia ; Casini, Antonio ; Montagna, Claudia...
Nature Communications. 11 (2020) 1 - p. , 2020

Link: https://doi.org/10.1038/..

9

Gene Therapy for Cystic Fibrosis: Progress and Challenges o..:

Maule, Giulia ; Arosio, Daniele ; Cereseto, Anna
International Journal of Molecular Sciences. 21 (2020) 11 - p. 3903 , 2020

Link: https://doi.org/10.3390/..

10

Allele specific repair of splicing mutations in cystic fibr..:

Maule, Giulia ; Casini, Antonio ; Montagna, Claudia...
Nature Communications. 10 (2019) 1 - p. , 2019

Link: https://doi.org/10.1038/..

11

A highly specific SpCas9 variant is identified by in vivo s..:

Casini, Antonio ; Olivieri, Michele ; Petris, Gianluca...
Nature Biotechnology. 36 (2018) 3 - p. 265-271 , 2018

Link: https://doi.org/10.1038/..

12

VSV-G-Enveloped Vesicles for Traceless Delivery of CRISPR-C..:

Montagna, Claudia ; Petris, Gianluca ; Casini, Antonio...
Molecular Therapy - Nucleic Acids. 12 (2018) - p. 453-462 , 2018

Link: https://doi.org/10.1016/..

13

Combination of lentiviral and genome editing technologies f..:

Ramadier, Sophie ; Chalumeau, Anne ; Felix, Tristan...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.ymthe.2021.08.019. , 2022

Link: https://hal.science/hal-..

14

Base-editing-mediated dissection of a γ-globin cis-regulato..:

Antoniou, Panagiotis ; Hardouin, Giulia ; Martinucci, Pierre...
info:eu-repo/semantics/altIdentifier/doi/10.1038/s41467-022-34493-1. , 2022

Link: https://mnhn.hal.science..

15

Base-editing-mediated dissection of a γ-globin cis-regulato..:

Antoniou, Panagiotis ; Hardouin, Giulia ; Martinucci, Pierre...
info:eu-repo/semantics/altIdentifier/doi/10.1038/s41467-022-34493-1. , 2022

Link: https://mnhn.hal.science..