E-LIB Suche - Ergebnisse für: Nidhi, Fnu

1

lentiviral gene therapy for mucopolysaccharidosis type IVA:

Celik, Betul ; Rintz, Estera ; Nidhi, Fnu..
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107789 , 2024

Link: https://doi.org/10.1016/..

2

Assessment of an iron oxide-coupled CRISPR/nCas9 gene editi..:

Leal, Andres F. ; Celik, Betul ; Nidhi, Fnu...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107933 , 2024

Link: https://doi.org/10.1016/..

3

Bone Growth Induction in Mucopolysaccharidosis IVA Mouse:

Rintz, Estera ; Herreño-Pachón, Angélica María ; Celik, Betul...
International Journal of Molecular Sciences. 24 (2023) 12 - p. 9890 , 2023

Link: https://doi.org/10.3390/..

4

Lentiviral gene therapy for mucopolysaccharidosis type IVA:

Celik, Betul ; Rintz, Estera ; Nidhi, Fnu..
Molecular Genetics and Metabolism. 138 (2023) 2 - p. 107047 , 2023

Link: https://doi.org/10.1016/..

5

Adeno-associated virus-based gene therapy delivering combin..:

Rintz, Estera ; Celik, Betul ; Fnu, Nidhi...
Molecular Therapy - Nucleic Acids. 35 (2024) 2 - p. 102211 , 2024

Link: https://doi.org/10.1016/..

6

The landscape of CRISPR/Cas9 for inborn errors of metabolis:

Leal, Andrés Felipe ; Fnu, Nidhi ; Benincore-Flórez, Eliana...
Molecular Genetics and Metabolism. 138 (2023) 1 - p. 106968 , 2023

Link: https://doi.org/10.1016/..

7

Iron oxide-coupled CRISPR-nCas9-based genome editing assess..:

Leal, Andrés Felipe ; Celik, Betul ; Fnu, Nidhi...
Molecular Therapy - Methods & Clinical Development. 31 (2023) - p. 101153 , 2023

Link: https://doi.org/10.1016/..

8

Sex Difference Leads to Differential Gene Expression Patter..:

Piechnik, Matthew ; Amendum, Paige C. ; Sawamoto, Kazuki...
International Journal of Molecular Sciences. 23 (2022) 20 - p. 12693 , 2022

Link: https://doi.org/10.3390/..

9

Glucosamine amends CNS pathology in mucopolysaccharidosis I..:

Pan, Xuefang ; Taherzadeh, Mahsa ; Bose, Poulomee...
Journal of Experimental Medicine. 219 (2022) 8 - p. , 2022

Link: https://doi.org/10.1084/..

10

Bone Growth Induction in Mucopolysaccharidosis IVA Mouse:

Rintz, Estera ; Herreño-Pachón, Angélica María ; Celik, Betul...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC10298227/. , 2023

Link: http://www.ncbi.nlm.nih...

11

Bone Growth Induction in Mucopolysaccharidosis IVA Mouse:

Rintz, Estera ; Herreño-Pachón, Angélica María ; Celik, Betul...
https://jdc.jefferson.edu/pedsfp/139. , 2023

Link: https://jdc.jefferson.ed..

12

Sex Difference Leads to Differential Gene Expression Patter..:

Matthew Piechnik ; Paige C. Amendum ; Kazuki Sawamoto...
Molecular Pathology, Diagnostics, and Therapeutics. , 2022

Link: https://doi.org/10.3390/..

13

Sex Difference Leads to Differential Gene Expression Patter..:

Matthew Piechnik ; Paige C. Amendum ; Kazuki Sawamoto...
https://www.mdpi.com/1422-0067/23/20/12693. , 2022

Link: https://doi.org/10.3390/..

14

Bone Growth Induction in Mucopolysaccharidosis IVA Mouse:

Estera Rintz ; Angélica María Herreño-Pachón ; Betul Celik...
Molecular Pathology, Diagnostics, and Therapeutics. , 2023

Link: https://doi.org/10.3390/..

15

Iron Oxide-Coupled CRISPR-nCas9-based Genome Editing Assess..:

Leal, Andrés ; Celik, Betul ; Fnu, Nidhi..
https://jdc.jefferson.edu/pedsfp/146. , 2023

Link: https://jdc.jefferson.ed..