E-LIB Suche - Ergebnisse für: Piguet, Françoise

1

Intravenous gene therapy using AAVPHP.eB for metachromatic ..:

Audouard, Emilie ; Banchi, Elena Gaia ; Alonso, Rafael...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107758 , 2024

Link: https://doi.org/10.1016/..

2

Cell-based device provides effective therapeutic strategy t..:

Audouard, Emilie ; Banchi, Elena Gaia ; Alonso, Rafael...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107759 , 2024

Link: https://doi.org/10.1016/..

3

Development and validation of a novel AAV gene therapy for ..:

Banchi, Elena Gaia ; Alonso, Rafael ; Jacquot, Sylvie...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107768 , 2024

Link: https://doi.org/10.1016/..

4

Dose-response evaluation of intravenous gene therapy in a s..:

Audouard, Emilie ; Khefif, Nicolas ; Mansat, Charlotte...
Molecular Therapy - Methods & Clinical Development. 32 (2024) 2 - p. 101248 , 2024

Link: https://doi.org/10.1016/..

5

Cholesterol redistribution triggered by CYP46A1 gene therap..:

Nunes, Maria João ; Carvalho, Andreia Neves ; Reis, Joana...
Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease. 1870 (2024) 3 - p. 166993 , 2024

Link: https://doi.org/10.1016/..

6

Modulation of Brain Cholesterol Metabolism through CYP46A1 ..:

Audouard, Emilie ; Khefif, Nicolas ; Gillet-Legrand, Béatrix...
Pharmaceutics. 16 (2024) 6 - p. 756 , 2024

Link: https://doi.org/10.3390/..

7

Development and validation of a novel adeno-associated vira..:

Ballout, Nissrine ; Verdu, Léna ; Santiago, Christophe...
Molecular Genetics and Metabolism. 138 (2023) 2 - p. 107019 , 2023

Link: https://doi.org/10.1016/..

8

Gene therapy for neurodegenerative disorders in children: d..:

Boespflug-Tanguy, Odile ; Sevin, Caroline ; Piguet, Francoise
Archives de Pédiatrie. 30 (2023) 8 - p. 8S32-8S40 , 2023

Link: https://doi.org/10.1016/..

9

Bioelectronic cell-based device provides a strategy for the..:

Audouard, Emilie ; Michel, Fanny ; Pierroz, Vanessa...
Journal of Controlled Release. 352 (2022) - p. 994-1008 , 2022

Link: https://doi.org/10.1016/..

10

Nouvelles approches de la thérapie génique:

Piguet, Françoise
Revue Neurologique. 178 (2022) - p. S175 , 2022

Link: https://doi.org/10.1016/..

11

AAV‐delivered diacylglycerol kinase DGKk achieves long‐term..:

Habbas, Karima ; Cakil, Oktay ; Zámbó, Boglárka...
EMBO Molecular Medicine. 14 (2022) 5 - p. , 2022

Link: https://doi.org/10.15252..

12

Optimized Protocol for Subcutaneous Implantation of Encapsu..:

Audouard, Emilie ; Rousselot, Lisa ; Folcher, Marc..
Frontiers in Bioengineering and Biotechnology. 9 (2021) - p. , 2021

Link: https://doi.org/10.3389/..

13

SCA7 Mouse Cerebellar Pathology Reveals Preferential Downre..:

Niewiadomska-Cimicka, Anna ; Doussau, Frédéric ; Perot, Jean-Baptiste...
The Journal of Neuroscience. 41 (2021) 22 - p. 4910-4936 , 2021

Link: https://doi.org/10.1523/..

14

Complete Correction of Brain and Spinal Cord Pathology in M..:

Audouard, Emilie ; Oger, Valentin ; Meha, Béatrix...
Frontiers in Molecular Neuroscience. 14 (2021) - p. , 2021

Link: https://doi.org/10.3389/..

15

Optimizing PCR for Mouse Genotyping: Recommendations for Re..:

Jacquot, Sylvie ; Chartoire, Nathalie ; Piguet, Françoise..
Current Protocols in Mouse Biology. 9 (2019) 4 - p. , 2019

Link: https://doi.org/10.1002/..