E-LIB Suche - Ergebnisse für: Podetz-Pedersen, Kelly M

1

Non-invasive intravenous administration of AAV9 transducing..:

Laoharawee, Kanut ; Podetz-Pedersen, Kelly M. ; Nguyen, Tam T....
Molecular Genetics and Metabolism Reports. 34 (2023) - p. 100956 , 2023

Link: https://doi.org/10.1016/..

2

Comparative Effectiveness of Intracerebroventricular, Intra..:

Belur, Lalitha R. ; Romero, Megan ; Lee, Junggu...
Frontiers in Molecular Neuroscience. 14 (2021) - p. , 2021

Link: https://doi.org/10.3389/..

3

Intravenous delivery for treatment of mucopolysaccharidosis..:

Belur, Lalitha R. ; Podetz-Pedersen, Kelly M. ; Tran, Thuy An...
Molecular Genetics and Metabolism Reports. 24 (2020) - p. 100604 , 2020

Link: https://doi.org/10.1016/..

4

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler ..:

Ou, Li ; DeKelver, Russell C. ; Rohde, Michelle...
Molecular Therapy. 27 (2019) 1 - p. 178-187 , 2019

Link: https://doi.org/10.1016/..

5

Dose-Dependent Prevention of Metabolic and Neurologic Disea..:

Laoharawee, Kanut ; DeKelver, Russell C. ; Podetz-Pedersen, Kelly M....
Molecular Therapy. 26 (2018) 4 - p. 1127-1136 , 2018

Link: https://doi.org/10.1016/..

6

Recovery of neurologic function in mucopolysaccharidosis ty..:

Belur, Lalitha ; Podetz-Pedersen, Kelly M ; Low, Walter C.
Molecular Genetics and Metabolism. 120 (2017) 1-2 - p. S26 , 2017

Link: https://doi.org/10.1016/..

7

Neurologic improvement in a mouse model of Hunter syndrome ..:

Podetz-Pedersen, Kelly M ; Laoharawee, Kanut ; Nguyen, Tam T...
Molecular Genetics and Metabolism. 120 (2017) 1-2 - p. S107-S108 , 2017

Link: https://doi.org/10.1016/..

8

Relative effectiveness of different routes of AAV administr..:

Scott McIvor, R. ; Kozarsky, Karen ; Laoharawee, Kanut...
Molecular Genetics and Metabolism. 120 (2017) 1-2 - p. S93 , 2017

Link: https://doi.org/10.1016/..

9

ZFN-mediated correction of murine MPS I model by expression..:

Ou, Li ; DeKelver, Russell ; Tom, Susan...
Molecular Genetics and Metabolism. 117 (2016) 2 - p. S89 , 2016

Link: https://doi.org/10.1016/..

10

Intranasal gene delivery of AAV9 iduronidase: A non-invasiv..:

Belur, Lalitha ; Buckvold, Megan ; Podetz-Pedersen, Kelly M....
Molecular Genetics and Metabolism. 117 (2016) 2 - p. S26 , 2016

Link: https://doi.org/10.1016/..

11

ZFN-mediated in vivo genome editing results in supraphysiol..:

DeKelver, Russell ; Laoharawee, Kanut ; Tom, Susan...
Molecular Genetics and Metabolism. 117 (2016) 2 - p. S40 , 2016

Link: https://doi.org/10.1016/..

12

25. Intranasal Gene Delivery of AAV Iduronidase: An Effecti..:

Belur, Lalitha ; Buckvold, Megan ; Podetz-Pedersen, Kelly M....
Molecular Therapy. 24 (2016) - p. S12 , 2016

Link: https://doi.org/10.1016/..

13

Gene delivery and biodistribution following intravenous adm..:

Belur, Lalitha ; Tran, Thuy An ; Podetz-Pedersen, Kelly M....
Molecular Genetics and Metabolism. 117 (2016) 2 - p. S26 , 2016

Link: https://doi.org/10.1016/..

14

A Broad Range of Dose Optima Achieve High-level, Long-term ..:

Podetz-Pedersen, Kelly M ; Olson, Erik R ; Somia, Nikunj V..
Molecular Therapy - Nucleic Acids. 5 (2016) - p. e279 , 2016

Link: https://doi.org/10.1038/..

15

369. AAV9 Mediated Correction of Iduronate-2-Sulfatase Defi..:

Laoharawee, Kanut ; Podetz-Pedersen, Kelly M. ; Kitto, Kelley...
Molecular Therapy. 23 (2015) - p. S146 , 2015

Link: https://doi.org/10.1016/..