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Przybilla, Michael
112  Ergebnisse:
Personensuche X
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1

Optimal stoichiometry of CRISPR-Cas9 components in the PS G..:

Przybilla, Michael J. ; Saveraid, Hanna ; Ou, Li.
Molecular Genetics and Metabolism.  141 (2024)  2 - p. 108005 , 2024
Link: https://doi.org/10.1016/..
 
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2

Drugging transcription factors with small activating RNAs: ..:

Habib, Nagy ; Reebye, Vikash ; Vanezis, Konstantinos...
Molecular Genetics and Metabolism.  138 (2023)  2 - p. 107134 , 2023
Link: https://doi.org/10.1016/..
 
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3

Treating murine Hurler syndrome utilizing small-activating ..:

Przybilla, Michael J. ; Reebye, Vikash ; Vanezis, Konstantinos...
Molecular Genetics and Metabolism.  138 (2023)  2 - p. 107279 , 2023
Link: https://doi.org/10.1016/..
 
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4

Identification of a novel fusion Iduronidase with improved ..:

Kim, Sarah ; Przybilla, Michael J. ; Whitley, Chester B....
Molecular Genetics and Metabolism Reports.  33 (2022)  - p. 100917 , 2022
Link: https://doi.org/10.1016/..
 
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5

Prevention of murine GM1-gangliosidosis following heterotop..:

Przybilla, Michael ; Sidhu, Rohini ; Kell, Pamela...
Molecular Genetics and Metabolism.  135 (2022)  2 - p. S101 , 2022
Link: https://doi.org/10.1016/..
 
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6

Examination of a blood-brain barrier targeting β-galactosid..:

Przybilla, Michael J. ; Stewart, Christine ; Carlson, Timothy W....
Molecular Genetics and Metabolism Reports.  27 (2021)  - p. 100748 , 2021
Link: https://doi.org/10.1016/..
 
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7

Immunogenicity, genotoxicity, and efficacy of PS gene editi..:

Ou, Li ; Przybilla, Michael ; Kim, Sarah..
Molecular Genetics and Metabolism.  132 (2021)  2 - p. S81 , 2021
Link: https://doi.org/10.1016/..
 
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8

Examination of a blood-brain barrier targeting β-galactosid..:

Przybilla, Michael ; Stewart, Christine ; Carlson, Timothy...
Molecular Genetics and Metabolism.  132 (2021)  2 - p. S88 , 2021
Link: https://doi.org/10.1016/..
 
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9

PS gene editing with a novel HEXO construct to treat both T..:

Ou, Li ; Przybilla, Michael ; Kim, Sarah..
Molecular Genetics and Metabolism.  132 (2021)  2 - p. S80-S81 , 2021
Link: https://doi.org/10.1016/..
 
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10

Gene editing to treat GM1-gangliosidosis by heterotopic ins..:

Przybilla, Michael ; Ou, Li ; Jarnes-Utz, Jeanine R..
Molecular Genetics and Metabolism.  129 (2020)  2 - p. S131 , 2020
Link: https://doi.org/10.1016/..
 
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11

Correction of both Tay-Sachs and Sandhoff diseases with the..:

Ou, Li ; Przybilla, Michael ; Tăbăran, Alexandru-Flaviu...
Molecular Genetics and Metabolism.  129 (2020)  2 - p. S125 , 2020
Link: https://doi.org/10.1016/..
 
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12

A novel gene editing system to treat both Tay–Sachs and San..:

Ou, Li ; Przybilla, Michael J. ; Tăbăran, Alexandru-Flaviu...
Gene Therapy.  27 (2020)  5 - p. 226-236 , 2020
Link: https://doi.org/10.1038/..
 
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13

SAAMP 3.0©: Computational biology to predict the phenotype ..:

Tan, Xinze ; Zhang, Xiangyu ; Przybilla, Michael..
Molecular Genetics and Metabolism.  129 (2020)  2 - p. S150 , 2020
Link: https://doi.org/10.1016/..
 
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14

Liver-targeting gene editing achieves significant neurologi..:

Ou, Li ; Przybilla, Michael ; Ahlat, Ozan...
Molecular Genetics and Metabolism.  129 (2020)  2 - p. S124-S125 , 2020
Link: https://doi.org/10.1016/..
 
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15

A Highly Efficacious PS Gene Editing System Corrects Metabo..:

Ou, Li ; Przybilla, Michael J. ; Ahlat, Ozan...
Molecular Therapy.  28 (2020)  6 - p. 1442-1454 , 2020
Link: https://doi.org/10.1016/..
 
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