E-LIB Suche - Ergebnisse für: Rocca, Celine J.

1

Novel insights advancing the understanding of renal Fanconi..:

Khare, Veenita ; Rocca, Celine J. ; Mishra, Priyanka...
Molecular Genetics and Metabolism. 141 (2024) 2 - p. 107916 , 2024

Link: https://doi.org/10.1016/..

2

Hematopoietic stem and progenitors cells gene editing: Beyo..:

Buffa, Valentina ; Alvarez Vargas, José Roberto ; Galy, Anne..
Frontiers in Genome Editing. 4 (2023) - p. , 2023

Link: https://doi.org/10.3389/..

3

Lentiviral standards to determine the sensitivity of assays..:

Corre, Guillaume ; Seye, Ababacar ; Frin, Sophie...
Gene Therapy. 29 (2022) 9 - p. 536-543 , 2022

Link: https://doi.org/10.1038/..

4

CRISPR-Cas9 Gene Editing of Hematopoietic Stem Cells from P..:

Rocca, Celine J. ; Rainaldi, Joseph N. ; Sharma, Jay...
Molecular Therapy - Methods & Clinical Development. 17 (2020) - p. 1026-1036 , 2020

Link: https://doi.org/10.1016/..

5

New interaction between galectin-3 and cystinosin reveals a..:

Lobry, Tatiana ; Miller, Roy ; Nevo, Nathalie...
Molecular Genetics and Metabolism. 123 (2018) 2 - p. S88 , 2018

Link: https://doi.org/10.1016/..

6

Potential use of stem cells as a therapy for cystinosis:

Rocca, Celine J. ; Cherqui, Stephanie
Pediatric Nephrology. 34 (2018) 6 - p. 965-973 , 2018

Link: https://doi.org/10.1007/..

7

Towards a phase I clinical trial for autologous hematopoiet..:

Lobry, Tatiana ; Sharma, Jay ; Ur, Sarah...
Molecular Genetics and Metabolism. 120 (2017) 1-2 - p. S86 , 2017

Link: https://doi.org/10.1016/..

8

Cystinosin, the small GTPase Rab11, and the Rab7 effector R..:

Zhang, Jinzhong ; Johnson, Jennifer L. ; He, Jing...
Journal of Biological Chemistry. 292 (2017) 25 - p. 10328-10346 , 2017

Link: https://doi.org/10.1074/..

9

32. Towards a Phase I Clinical Trial for Cystinosis:

Lobry, Tatiana ; Sharma, Jay ; Ur, Sarah...
Molecular Therapy. 24 (2016) - p. S14-S15 , 2016

Link: https://doi.org/10.1016/..

10

350. Kidney-Directed Gene Therapy for Murine Glycogen Stora..:

Lee, Youngmok ; Bae, Seongho ; Rocca, Celine J....
Molecular Therapy. 24 (2016) - p. S140 , 2016

Link: https://doi.org/10.1016/..

11

163. Hematopoietic Stem Cells Transplantation Can Normalize..:

Chevronnay, Heloise P. Gaide ; Janssens, Virginie ; Van Der Smissen, Patrick...
Molecular Therapy. 24 (2016) - p. S64 , 2016

Link: https://doi.org/10.1016/..

12

84. Pharmacology/Toxicology Studies for Gene-Modified Hemat..:

Lobry, Tatiana ; Ur, Sarah ; Lau, Athena...
Molecular Therapy. 23 (2015) - p. S36-S37 , 2015

Link: https://doi.org/10.1016/..

13

708. Treatment of Inherited Eye Defects By Systemic Hematop..:

Rocca, Celine J. ; Kreymerman, Alexander ; Ur, Sarah N....
Molecular Therapy. 23 (2015) - p. S282 , 2015

Link: https://doi.org/10.1016/..

14

BRCA2 is needed for both repair and cell cycle arrest in ma..:

Rocca, Céline J ; Soares, Daniele G ; Bouzid, Hana...
Cell Cycle. 14 (2015) 13 - p. 2080-2090 , 2015

Link: https://doi.org/10.1080/..

15

Impairment of chaperone‐mediated autophagy leads to selecti..:

Napolitano, Gennaro ; Johnson, Jennifer L ; He, Jing...
EMBO Molecular Medicine. 7 (2015) 2 - p. 158-174 , 2015

Link: https://doi.org/10.15252..