E-LIB Suche - Ergebnisse für: Rodino-Klapac, L.

1

P17 Safety and efficacy of pre-treatment with imlifidase pr..:

Potter, R. ; Khan, S. ; Snedeker, J....
Neuromuscular Disorders. 33 (2023) - p. S101 , 2023

Link: https://doi.org/10.1016/..

2

P54 T-cell response to SRP-9001 dystrophin transgene in a p..:

Khan, S. ; Haegel, H. ; Hollenstein, A....
Neuromuscular Disorders. 33 (2023) - p. S72 , 2023

Link: https://doi.org/10.1016/..

3

P23 Evaluation of safety parameters and dystrophin expressi..:

Potter, R. ; Olson, G Cooper ; Smith, L....
Neuromuscular Disorders. 33 (2023) - p. S102-S103 , 2023

Link: https://doi.org/10.1016/..

4

P.128 Integrated analyses of data from clinical trials of d..:

Zaidman, C. ; Shieh, P. ; Proud, C....
Neuromuscular Disorders. 32 (2022) - p. S101 , 2022

Link: https://doi.org/10.1016/..

5

P.129 One-year data from ENDEAVOR, a phase 1b trial of dela..:

Zaidman, C. ; Proud, C. ; McDonald, C....
Neuromuscular Disorders. 32 (2022) - p. S101 , 2022

Link: https://doi.org/10.1016/..

6

P.170 Safety, β-sarcoglycan expression, and functional outc..:

Rodino-Klapac, L. ; Pozsgai, E. ; Lewis, S....
Neuromuscular Disorders. 32 (2022) - p. S116 , 2022

Link: https://doi.org/10.1016/..

7

P.134a Phase 1/2a trial of delandistrogene moxeparvovec in ..:

Mendell, J. ; Sahenk, Z. ; Lehman, K....
Neuromuscular Disorders. 32 (2022) - p. S102-S103 , 2022

Link: https://doi.org/10.1016/..

8

VP.82 PK/PD modelling to inform clinical development of an ..:

East, L. ; Potter, R. ; Snedeker, J....
Neuromuscular Disorders. 32 (2022) - p. S127 , 2022

Link: https://doi.org/10.1016/..

9

P.197 Evaluating pharmacology and efficacy of delandistroge..:

Potter, R. ; Wier, C. ; Cooper-Olson, G....
Neuromuscular Disorders. 32 (2022) - p. S127 , 2022

Link: https://doi.org/10.1016/..

10

LGMD:

Rodino-Klapac, L. ; Pozsgai, E. ; Lewis, S....
Neuromuscular Disorders. 31 (2021) - p. S105 , 2021

Link: https://doi.org/10.1016/..

11

CLINICAL TRIAL HIGHLIGHTS:

Mendell, J. ; Shieh, P. ; Sahenk, Z....
Neuromuscular Disorders. 31 (2021) - p. S127 , 2021

Link: https://doi.org/10.1016/..

12

DMD - TREATMENT:

Mendell, J. ; Sahenk, Z. ; Lehman, K....
Neuromuscular Disorders. 31 (2021) - p. S91 , 2021

Link: https://doi.org/10.1016/..

13

DMD – ANIMAL MODELS:

Peterson, E. ; Potter, R. ; Griffin, D....
Neuromuscular Disorders. 31 (2021) - p. S78 , 2021

Link: https://doi.org/10.1016/..

14

DMD - TREATMENT:

Zaidman, C. ; Proud, C. ; McDonald, C....
Neuromuscular Disorders. 31 (2021) - p. S95 , 2021

Link: https://doi.org/10.1016/..

15

LIMB GIRDLE MUSCULAR DYSTROPHIES:

Pozsgai, E. ; Griffin, D. ; Peterson, E....
Neuromuscular Disorders. 30 (2020) - p. S86-S87 , 2020

Link: https://doi.org/10.1016/..