E-LIB Suche - Ergebnisse für: Santilli, Giorgia

1

Hematopoietic stem cell gene editing rescues B-cell develop..:

Bahal, Sameer ; Zinicola, Marta ; Moula, Shefta E...
Journal of Allergy and Clinical Immunology. 154 (2024) 1 - p. 195-208.e8 , 2024

Link: https://doi.org/10.1016/..

2

Myelodysplasia and transgene inactivation in X-CGD-γ retrov..:

Whittaker, Thomas E. ; Santilli, Giorgia
Molecular Therapy. 31 (2023) 12 - p. 3367-3368 , 2023

Link: https://doi.org/10.1016/..

3

AAV capsid bioengineering in primary human retina models:

Westhaus, Adrian ; Eamegdool, Steven S. ; Fernando, Milan...
Scientific Reports. 13 (2023) 1 - p. , 2023

Link: https://doi.org/10.1038/..

4

Definitive Treatments for Chronic Granulomatous Disease wit..:

, In: NADPH Oxidases Revisited: From Function to Structure,

Santilli, Giorgia ; Thrasher, Adrian J. - p. 557-572 , 2023

Link: https://doi.org/10.1007/..

5

An improved medium formulation for efficient ex vivo gene e..:

Rai, Rajeev ; Naseem, Asma ; Vetharoy, Winston...
Molecular Therapy - Methods & Clinical Development. 29 (2023) - p. 58-69 , 2023

Link: https://doi.org/10.1016/..

6

Gene Editing in Human Haematopoietic Stem Cells for the Tre..:

Bahal, Sameer ; Karaxhuku, Klesti ; Santilli, Giorgia
Molecular Diagnosis & Therapy. 27 (2022) 1 - p. 15-28 , 2022

Link: https://doi.org/10.1007/..

7

Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Cli..:

Piras, Giuseppa ; Montiel-Equihua, Claudia ; Chan, Yee-Ka Agnes...
Molecular Therapy - Methods & Clinical Development. 18 (2020) - p. 558-570 , 2020

Link: https://doi.org/10.1016/..

8

WAS Promoter-Driven Lentiviral Vectors Mimic Closely the Lo..:

Muñoz, Pilar ; Tristán-Manzano, María ; Sánchez-Gilabert, Almudena...
Molecular Therapy - Methods & Clinical Development. 19 (2020) - p. 220-235 , 2020

Link: https://doi.org/10.1016/..

9

Targeted gene correction of human hematopoietic stem cells ..:

Rai, Rajeev ; Romito, Marianna ; Rivers, Elizabeth...
Nature Communications. 11 (2020) 1 - p. , 2020

Link: https://doi.org/10.1038/..

10

Attenuation of Heparan Sulfate Proteoglycan Binding Enhance..:

Cabanes-Creus, Marti ; Westhaus, Adrian ; Navarro, Renina Gale...
Molecular Therapy - Methods & Clinical Development. 17 (2020) - p. 1139-1154 , 2020

Link: https://doi.org/10.1016/..

11

Lentiviral gene therapy rescues p47phox chronic granulomato..:

Schejtman, Andrea ; Aragão-Filho, Walmir Cutrim ; Clare, Simon...
Gene Therapy. 27 (2020) 9 - p. 459-469 , 2020

Link: https://doi.org/10.1038/..

12

Enhancing Lentiviral and Alpharetroviral Transduction of Hu..:

Schott, Juliane W. ; León-Rico, Diego ; Ferreira, Carolina B....
Molecular Therapy - Methods & Clinical Development. 14 (2019) - p. 134-147 , 2019

Link: https://doi.org/10.1016/..

13

EROS/CYBC1 mutations: Decreased NADPH oxidase function and ..:

Thomas, David C. ; Charbonnier, Louis-Marie ; Schejtman, Andrea...
Journal of Allergy and Clinical Immunology. 143 (2019) 2 - p. 782-785.e1 , 2019

Link: https://doi.org/10.1016/..

14

Codon-Optimization of Wild-Type Adeno-Associated Virus Caps..:

Cabanes-Creus, Marti ; Ginn, Samantha L. ; Amaya, Anais K....
Molecular Therapy - Methods & Clinical Development. 12 (2019) - p. 71-84 , 2019

Link: https://doi.org/10.1016/..

15

Pulmonary metastatic colonisation and granulomas in NOX2‐de..:

van der Weyden, Louise ; Speak, Anneliese O ; Swiatkowska, Agnieszka...
The Journal of Pathology. 246 (2018) 3 - p. 300-310 , 2018

Link: https://doi.org/10.1002/..