E-LIB Suche - Ergebnisse für: Sellier, Pauline

1

Hepatic expression of GAA results in enhanced enzyme bioava..:

Costa-Verdera, Helena ; Collaud, Fanny ; Riling, Christopher R....
Nature Communications. 12 (2021) 1 - p. , 2021

2

Liver expression of secretable GAA rescues advanced Pompe d..:

Cagin, Umut ; Puzzo, Francesco ; Gomez, Manuel Jose...
Molecular Genetics and Metabolism. 129 (2020) 2 - p. S36-S37 , 2020

Link: https://doi.org/10.1016/..

3

Rescue of Advanced Pompe Disease in Mice with Hepatic Expre..:

Cagin, Umut ; Puzzo, Francesco ; Gomez, Manuel Jose...
Molecular Therapy. 28 (2020) 9 - p. 2056-2072 , 2020

Link: https://doi.org/10.1016/..

4

Preclinical development of , an investigational liver-direc..:

Armour, Sean M. ; Nordin, Jayme M.L. ; Verdera, Helena Costa...
Molecular Genetics and Metabolism. 129 (2020) 2 - p. S22-S23 , 2020

Link: https://doi.org/10.1016/..

5

Gene therapy with secreted acid alpha-glucosidase rescues P..:

Colella, Pasqualina ; Sellier, Pauline ; Gomez, Manuel J....
EBioMedicine. 61 (2020) - p. 103052 , 2020

Link: https://doi.org/10.1016/..

6

Tandem promoter design confers tolerogenic and persistent t..:

Colella, Pasqualina ; Sellier, Pauline ; Costa-Verdera, Helena...
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S41 , 2019

Link: https://doi.org/10.1016/..

7

AAV Gene Transfer with Tandem Promoter Design Prevents Anti..:

Colella, Pasqualina ; Sellier, Pauline ; Costa Verdera, Helena...
Molecular Therapy - Methods & Clinical Development. 12 (2019) - p. 85-101 , 2019

Link: https://doi.org/10.1016/..

8

Latent TGF-beta-binding protein 4 modulates disease severit..:

Colella, Pasqualina ; Sellier, Pauline ; Cagin, Umut...
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S41 , 2019

Link: https://doi.org/10.1016/..

9

Functional, biochemical and transcriptional rescue of advan..:

Cagin, Umut ; Puzzo, Francesco ; Gomez, Manuel Jose...
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S35 , 2019

Link: https://doi.org/10.1016/..

10

Kininogen Cleavage Assay: Diagnostic Assistance for Kinin-M..:

Baroso, Rémi ; Sellier, Pauline ; Defendi, Federica...
PLOS ONE. 11 (2016) 9 - p. e0163958 , 2016

Link: https://doi.org/10.1371/..

11

C1 Inhibitor as a glycoprotein: The influence of polysaccha..:

Ghannam, Arije ; Sellier, Pauline ; Fain, Olivier...
Molecular Immunology. 71 (2016) - p. 161-165 , 2016

Link: https://doi.org/10.1016/..

12

Hepatic expression of GAA results in enhanced enzyme bioava..:

Costa-Verdera, Helena ; Collaud, Fanny ; Riling, Christopher R...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8568898/. , 2021

Link: http://www.ncbi.nlm.nih...

13

Hepatic expression of GAA results in enhanced enzyme bioava..:

Costa-Verdera, Helena ; Collaud, Fanny ; Riling, Christopher, R...
info:eu-repo/semantics/altIdentifier/doi/10.1038/s41467-021-26744-4. , 2021

Link: https://hal.sorbonne-uni..

14

Hepatic expression of GAA results in enhanced enzyme bioava..:

Costa-Verdera, Helena ; Collaud, Fanny ; Riling, Christopher, R...
info:eu-repo/semantics/altIdentifier/doi/10.1038/s41467-021-26744-4. , 2021

Link: https://hal.sorbonne-uni..

15

Hepatic expression of GAA results in enhanced enzyme bioava..:

Costa-Verdera, Helena ; Collaud, Fanny ; Riling, Christopher...
info:eu-repo/semantics/altIdentifier/doi/10.1038/s41467-021-26744-4. , 2021

Link: https://hal.sorbonne-uni..