E-LIB Suche - Ergebnisse für: Thrasher, Adrian

1

Valproic Acid Confers Functional Pluripotency to Human Amni..:

Moschidou, Dafni ; Mukherjee, Sayandip ; Blundell, Michael P....
Molecular Therapy. , 2024

2

Hematopoietic stem cell gene editing rescues B-cell develop..:

Bahal, Sameer ; Zinicola, Marta ; Moula, Shefta E...
Journal of Allergy and Clinical Immunology. 154 (2024) 1 - p. 195-208.e8 , 2024

Link: https://doi.org/10.1016/..

3

Anti-CD45 PBD-based antibody-drug conjugates are effective ..:

Yeung, Jenny ; Liao, Aiyin ; Shaw, Matthew...
Molecular Therapy. 32 (2024) 6 - p. 1672-1686 , 2024

Link: https://doi.org/10.1016/..

4

Design and validation of a GMP stem cell manufacturing prot..:

Ellison, Stuart ; Buckland, Karen ; Learmonth, Yuko...
Molecular Therapy - Methods & Clinical Development. 32 (2024) 2 - p. 101271 , 2024

Link: https://doi.org/10.1016/..

5

Evaluation of Mobilization, Apheresis, and Conditioning Reg..:

Duncan, Christine N. ; Orchard, Paul J. ; Eichler, Florian S....
Transplantation and Cellular Therapy. 30 (2024) 2 - p. S232-S233 , 2024

Link: https://doi.org/10.1016/..

6

Investigating adverse genomic and regulatory changes caused..:

Vaidyanathan, Sriram ; Kerschner, Jenny L. ; Paranjapye, Alekh...
Molecular Therapy - Nucleic Acids. 35 (2024) 1 - p. 102134 , 2024

Link: https://doi.org/10.1016/..

7

Sustained Efficacy and Safety in Adult and Pediatric Patien..:

Walters, Mark C. ; Thompson, Alexis A. ; Olson, Timothy S....
Transplantation and Cellular Therapy. 30 (2024) 2 - p. S230 , 2024

Link: https://doi.org/10.1016/..

8

Long-term Outcomes of 63 Patients with Transfusion-Dependen..:

Olson, Timothy S. ; Walters, Mark C. ; Kwiatkowski, Janet L....
Transplantation and Cellular Therapy. 29 (2023) 2 - p. S291-S292 , 2023

Link: https://doi.org/10.1016/..

9

AAV capsid bioengineering in primary human retina models:

Westhaus, Adrian ; Eamegdool, Steven S. ; Fernando, Milan...
Scientific Reports. 13 (2023) 1 - p. , 2023

Link: https://doi.org/10.1038/..

10

Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Pati..:

Booth, Claire ; Sevilla, Julian ; Rao, Gayatri...
Transplantation and Cellular Therapy. 29 (2023) 2 - p. S2-S3 , 2023

Link: https://doi.org/10.1016/..

11

Lentiviral-Mediated Gene Therapy for Patients with Fanconi ..:

Czechowicz, Agnieszka ; Sevilla, Julian ; Booth, Claire...
Transplantation and Cellular Therapy. 29 (2023) 2 - p. S89 , 2023

Link: https://doi.org/10.1016/..

12

Correction: The Tight Junction Associated Signalling Protei..:

Georgiadis, Anastasios ; Tschernutter, Marion ; Bainbridge, James W. B....
PLOS ONE. 18 (2023) 12 - p. e0295782 , 2023

Link: https://doi.org/10.1371/..

13

Definitive Treatments for Chronic Granulomatous Disease wit..:

, In: NADPH Oxidases Revisited: From Function to Structure,

Santilli, Giorgia ; Thrasher, Adrian J. - p. 557-572 , 2023

Link: https://doi.org/10.1007/..

14

Severe hematopoietic stem cell inflammation compromises chr..:

Sobrino, Steicy ; Magnani, Alessandra ; Semeraro, Michaela...
Cell Reports Medicine. 4 (2023) 2 - p. 100919 , 2023

Link: https://doi.org/10.1016/..

15

Access to gene therapy for rare diseases when commercializa..:

Fox, Thomas ; Bueren, Juan ; Candotti, Fabio...
Nature Medicine. 29 (2023) 3 - p. 518-519 , 2023

Link: https://doi.org/10.1038/..