E-LIB Suche - Ergebnisse für: Urbinati, Fabrizia

1

AAV8 gene therapy reverses cardiac pathology and prevents e..:

Chang, Joshua C. ; Ryan, Molly R. ; Stark, Marie C....
Molecular Therapy - Methods & Clinical Development. 32 (2024) 1 - p. 101193 , 2024

Link: https://doi.org/10.1016/..

2

High-throughput transcriptome analyses from ASPIRO, a phase..:

Andreoletti, Gaia ; Romano, Oriana ; Chou, Hsin-Jung...
The American Journal of Human Genetics. 110 (2023) 10 - p. 1648-1660 , 2023

Link: https://doi.org/10.1016/..

3

Pre-clinical Development of a Lentiviral Vector Expressing ..:

Poletti, Valentina ; Urbinati, Fabrizia ; Charrier, Sabine...
Molecular Therapy - Methods & Clinical Development. 11 (2018) - p. 167-179 , 2018

Link: https://doi.org/10.1016/..

4

Improving Gene Therapy Efficiency through the Enrichment of..:

Masiuk, Katelyn E. ; Brown, Devin ; Laborada, Jennifer...
Molecular Therapy. 25 (2017) 9 - p. 2163-2175 , 2017

Link: https://doi.org/10.1016/..

5

Preclinical studies for a phase 1 clinical trial of autolog..:

Urbinati, Fabrizia ; Wherley, Jennifer ; Geiger, Sabine...
Cytotherapy. 19 (2017) 9 - p. 1096-1112 , 2017

Link: https://doi.org/10.1016/..

6

CRISPR/Cas9-Mediated Correction of the Sickle Mutation in H..:

Hoban, Megan D ; Lumaquin, Dianne ; Kuo, Caroline Y...
Molecular Therapy. 24 (2016) 9 - p. 1561-1569 , 2016

Link: https://doi.org/10.1038/..

7

230. Designing High-Titer Lentiviral Vectors for Gene Thera..:

Urbinati, Fabrizia ; Poletti, Valentina ; Fernandez, Beatriz Campo...
Molecular Therapy. 24 (2016) - p. S90 , 2016

Link: https://doi.org/10.1016/..

8

Reactivating Fetal Hemoglobin Expression in Human Adult Ery..:

Bjurström, Carmen F ; Mojadidi, Michelle ; Phillips, John...
Molecular Therapy - Nucleic Acids. 5 (2016) - p. e351 , 2016

Link: https://doi.org/10.1038/..

9

Enrichment of Human Hematopoietic Stem/Progenitor Cells Fac..:

Baldwin, Kismet ; Urbinati, Fabrizia ; Romero, Zulema...
Stem Cells. 33 (2015) 5 - p. 1532-1542 , 2015

Link: https://doi.org/10.1002/..

10

The human ankyrin 1 promoter insulator sustains gene expres..:

Romero, Zulema ; Campo-Fernandez, Beatriz ; Wherley, Jennifer...
Molecular Therapy - Methods & Clinical Development. 2 (2015) - p. 15012 , 2015

Link: https://doi.org/10.1038/..

11

Potentially therapeutic levels of anti-sickling globin gene..:

Urbinati, Fabrizia ; Hargrove, Phillip W. ; Geiger, Sabine...
Experimental Hematology. 43 (2015) 5 - p. 346-351 , 2015

Link: https://doi.org/10.1016/..

12

115. Correction of the Sickle-Cell Disease Mutation in Huma..:

Hoban, Megan D. ; Mendel, Matthew C. ; Romero, Zulema...
Molecular Therapy. 23 (2015) - p. S48 , 2015

Link: https://doi.org/10.1016/..

13

The 3′ Region of the Chicken Hypersensitive Site-4 Insulato..:

Arumugam, Paritha I. ; Urbinati, Fabrizia ; Velu, Chinavenmeni S....
PLoS ONE. 4 (2009) 9 - p. e6995 , 2009

Link: https://doi.org/10.1371/..

14

Genotoxic Potential of Lineage-specific Lentivirus Vectors ..:

Arumugam, Paritha I ; Higashimoto, Tomoyasu ; Urbinati, Fabrizia...
Molecular Therapy. 17 (2009) 11 - p. 1929-1937 , 2009

Link: https://doi.org/10.1038/..

15

Mechanism of Reduction in Titers From Lentivirus Vectors Ca..:

Urbinati, Fabrizia ; Arumugam, Paritha ; Higashimoto, Tomoyasu...
Molecular Therapy. 17 (2009) 9 - p. 1527-1536 , 2009

Link: https://doi.org/10.1038/..