E-LIB Suche - Ergebnisse für: Verdera, Helena Costa

1

Preclinical development of , an investigational liver-direc..:

Armour, Sean M. ; Nordin, Jayme M.L. ; Verdera, Helena Costa...
Molecular Genetics and Metabolism. 129 (2020) 2 - p. S22-S23 , 2020

Link: https://doi.org/10.1016/..

2

AAV Vector Immunogenicity in Humans: A Long Journey to Succ..:

Verdera, Helena Costa ; Kuranda, Klaudia ; Mingozzi, Federico
Molecular Therapy. 28 (2020) 3 - p. 723-746 , 2020

Link: https://doi.org/10.1016/..

3

Safety and efficacy evaluation of investigational liver gen..:

Armour, Sean M. ; Nordin, Jayme ; Puzzo, Francesco...
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S24 , 2019

Link: https://doi.org/10.1016/..

4

Role of Regulatory T Cell and Effector T Cell Exhaustion in..:

Poupiot, Jérôme ; Costa Verdera, Helena ; Hardet, Romain...
Molecular Therapy - Methods & Clinical Development. 15 (2019) - p. 83-100 , 2019

Link: https://doi.org/10.1016/..

5

AAV Gene Transfer with Tandem Promoter Design Prevents Anti..:

Colella, Pasqualina ; Sellier, Pauline ; Costa Verdera, Helena...
Molecular Therapy - Methods & Clinical Development. 12 (2019) - p. 85-101 , 2019

Link: https://doi.org/10.1016/..

6

Rescue of GSDIII Phenotype with Gene Transfer Requires Live..:

Vidal, Patrice ; Pagliarani, Serena ; Colella, Pasqualina...
Molecular Therapy. 26 (2018) 3 - p. 890-901 , 2018

Link: https://doi.org/10.1016/..

7

Antigen-selective modulation of AAV immunogenicity with tol..:

Meliani, Amine ; Boisgerault, Florence ; Hardet, Romain...
Nature Communications. 9 (2018) 1 - p. , 2018

Link: https://doi.org/10.1038/..

8

Cellular uptake of extracellular vesicles is mediated by cl..:

Costa Verdera, Helena ; Gitz-Francois, Jerney J. ; Schiffelers, Raymond M..
Journal of Controlled Release. 266 (2017) - p. 100-108 , 2017

Link: https://doi.org/10.1016/..

9

Engineering adeno-associated viral vectors to evade innate ..:

Chan, Ying Kai ; Wang, Sean K ; Chu, Colin J...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8409505/. , 2021

Link: http://www.ncbi.nlm.nih...

10

AAV Vector Immunogenicity in Humans: A Long Journey to Succ..:

Verdera, Helena Costa ; Kuranda, Klaudia ; Mingozzi, Federico
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC7054726/. , 2020

Link: http://www.ncbi.nlm.nih...

11

Hepatic expression of GAA results in enhanced enzyme bioava..:

Costa-Verdera, Helena ; Collaud, Fanny ; Riling, Christopher R....
Nature Communications. 12 (2021) 1 - p. , 2021

Link: https://doi.org/10.1038/..

12

Tandem promoter design confers tolerogenic and persistent t..:

Colella, Pasqualina ; Sellier, Pauline ; Costa-Verdera, Helena...
Molecular Genetics and Metabolism. 126 (2019) 2 - p. S41 , 2019

Link: https://doi.org/10.1016/..

13

Engineering adeno-associated viral vectors to evade innate ..:

Chan, Ying Kai ; Wang, Sean K ; Chu, Colin J...
Chan , Y K , Wang , S K , Chu , C J , Copland , D A , Letizia , A J , Costa Verdera , H , Chiang , J J , Sethi , M , Wang , M K , Neidermyer , W J , Chan , Y , Lim , E T , Graveline , A R , Sanchez , M , Boyd , R F , Vihtelic , T S , Inciong , R G C O , Slain , J M , Alphonse , P J , Xue , Y , Robinson-McCarthy , L R , Tam , J M , Jabbar , M H , Sahu , B , Adeniran , J F , Muhuri , M , Tai , P W L , Xie , J , Krause , T B , Vernet , A , Pezone , M , Xiao , R , Liu , T , Wang , W , Kaplan , H J , Gao , G , Dick , A D , Mingozzi , F , McCall , M A , Cepko , C L & Church , G M 2021 , ' Engineering adeno-associated viral vectors to evade innate immune and inflammatory responses ' , Science Translational Medicine , vol. 13 , no. 580 , eabd3438 . https://doi.org/10.1126/scitranslmed.abd3438. , 2021

Link: https://hdl.handle.net/1..

14

AAV Gene Transfer with Tandem Promoter Design Prevents Anti..:

Pasqualina Colella ; Pauline Sellier ; Helena Costa Verdera...
http://www.sciencedirect.com/science/article/pii/S2329050118301141. , 2019

Link: https://doi.org/10.1016/..

15

Role of Regulatory T Cell and Effector T Cell Exhaustion in..:

Poupiot, Jérôme ; Costa Verdera, Helena ; Hardet, Romain...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2019.08.012. , 2019

Link: https://hal.science/hal-..