E-LIB Suche - Ergebnisse für: Vidal, Patrice

1

Synergism of dual AAV gene therapy and rapamycin rescues GS..:

Jauze, Louisa ; Vie, Mallaury ; Miagoux, Quentin...
JCI Insight. 9 (2024) 11 - p. , 2024

2

A functional mini-GDE transgene corrects impairment in mode..:

Gardin, Antoine ; Rouillon, Jérémy ; Montalvo-Romeral, Valle...
Journal of Clinical Investigation. 134 (2024) 2 - p. , 2024

Link: https://doi.org/10.1172/..

3

Long-term correction of ornithine transcarbamylase deficien..:

De Sabbata, Giulia ; Boisgerault, Florence ; Guarnaccia, Corrado...
Molecular Therapy - Methods & Clinical Development. 20 (2021) - p. 169-180 , 2021

Link: https://doi.org/10.1016/..

4

Preclinical Development of an AAV8-hUGT1A1 Vector for the T..:

Collaud, Fanny ; Bortolussi, Giulia ; Guianvarc'h, Laurence...
Molecular Therapy - Methods & Clinical Development. 12 (2019) - p. 157-174 , 2019

Link: https://doi.org/10.1016/..

5

Rescue of GSDIII Phenotype with Gene Transfer Requires Live..:

Vidal, Patrice ; Pagliarani, Serena ; Colella, Pasqualina...
Molecular Therapy. 26 (2018) 3 - p. 890-901 , 2018

Link: https://doi.org/10.1016/..

6

158. Cryptic ATG Removal from Synthetic Introns Increase th..:

Ronzitti, Giuseppe ; Collaud, Fanny ; Bortolussi, Giulia...
Molecular Therapy. 24 (2016) - p. S62 , 2016

Link: https://doi.org/10.1016/..

7

A translationally optimized AAV-UGT1A1 vector drives safe a..:

Ronzitti, Giuseppe ; Bortolussi, Giulia ; van Dijk, Remco...
Molecular Therapy - Methods & Clinical Development. 3 (2016) - p. 16049 , 2016

Link: https://doi.org/10.1038/..

8

Long-term correction of ornithine transcarbamylase deficien..:

Sola, Marcelo Simon ; Kishimoto, Takashi Kei ; de Sabbata, Giulia...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2020.11.005. , 2021

Link: https://hal.sorbonne-uni..

9

Long-term correction of ornithine transcarbamylase deficien..:

Sola, Marcelo Simon ; Kishimoto, Takashi Kei ; de Sabbata, Giulia...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2020.11.005. , 2021

Link: https://hal.sorbonne-uni..

10

Long-term correction of ornithine transcarbamylase deficien..:

Sola, Marcelo Simon ; Kishimoto, Takashi Kei ; de Sabbata, Giulia...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2020.11.005. , 2021

Link: https://hal.sorbonne-uni..

11

Long-term correction of ornithine transcarbamylase deficien..:

Sola, Marcelo Simon ; Kishimoto, Takashi Kei ; De Sabbata, Giulia...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2020.11.005. , 2021

Link: https://hal.sorbonne-uni..

12

Preclinical Development of an AAV8-hUGT1A1 Vector for the T..:

Collaud, Fanny ; Bortolussi, Giulia ; Guianvarc'H, Laurence...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2018.12.011. , 2019

Link: https://univ-evry.hal.sc..

13

Preclinical Development of an AAV8-hUGT1A1 Vector for the T..:

Collaud, Fanny ; Bortolussi, Giulia ; Guianvarc'H, Laurence...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2018.12.011. , 2019

Link: https://univ-evry.hal.sc..

14

Preclinical Development of an AAV8-hUGT1A1 Vector for the T..:

Collaud, Fanny ; Bortolussi, Giulia ; Guianvarc'H, Laurence...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2018.12.011. , 2019

Link: https://univ-evry.hal.sc..

15

Preclinical Development of an AAV8-hUGT1A1 Vector for the T..:

Collaud, Fanny ; Bortolussi, Giulia ; Guianvarc'H, Laurence...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtm.2018.12.011. , 2019

Link: https://univ-evry.hal.sc..