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Henricson, Erik
129
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Online (129)
Mediatypes
Articles (Online) (71)
Bookchapter (Online) (3)
OpenAccess-fulltext (55)
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?
1
Eteplirsen Treatment for Duchenne Muscular Dystrophy: A Qua..:
Iff, Joel
;
Carmichael, Chloe
;
McKee, Stephanie
...
Advances in Therapy. 41 (2024) 8 - p. 3278-3298 , 2024
Link:
https://doi.org/10.1007/..
?
2
Findings from the Longitudinal CINRG Becker Natural History..:
Clemens, Paula R.
;
Gordish-Dressman, Heather
;
Niizawa, Gabriela
...
Journal of Neuromuscular Diseases. 11 (2024) 1 - p. 201-212 , 2024
Link:
https://doi.org/10.3233/..
?
3
269th ENMC international workshop: 10 years of clinical tri..:
Naarding, Karin J.
;
Stimpson, Georgia
;
Ward, Susan J.
...
Neuromuscular Disorders. 33 (2023) 11 - p. 897-910 , 2023
Link:
https://doi.org/10.1016/..
?
4
Dystrophinopathy and the brain: A parent project muscular d..:
Colvin, Mary K.
;
Truba, Natalie
;
Sorensen, Seth
..
Neuromuscular Disorders. 32 (2022) 11-12 - p. 935-944 , 2022
Link:
https://doi.org/10.1016/..
?
5
An Overview of Human Activity Recognition Using Wearable Se..:
, In:
Lecture Notes in Computer Science; Internet of Things – ICIOT 2021
,
Liu, Rex
;
Ramli, Albara Ah
;
Zhang, Huanle
.. - p. 1-14 , 2022
Link:
https://doi.org/10.1007/..
?
6
Disease Progression Stages and Burden in Patients with Duch..:
Iff, Joel
;
Zhong, Yi
;
Gupta, Deepshekhar
...
Advances in Therapy. 39 (2022) 6 - p. 2906-2919 , 2022
Link:
https://doi.org/10.1007/..
?
7
Rasch Analysis of the Pediatric Quality of Life Inventory 4..:
Landfeldt, Erik
;
Iff, Joel
;
Henricson, Erik
...
Value in Health. 24 (2021) 10 - p. 1490-1498 , 2021
Link:
https://doi.org/10.1016/..
?
8
The Minimal Clinical Important Difference (MCID) in Annual ..:
Duong, Tina
;
Canbek, Jennifer
;
Birkmeier, Marisa
...
Journal of Neuromuscular Diseases. 8 (2021) 6 - p. 939-948 , 2021
Link:
https://doi.org/10.3233/..
?
9
Delays in Progression of Duchenne Muscular Dystrophy with E..:
Iff, Joel
;
Gerrits, Charles
;
Birk, Erica
...
Neurology. 94 (2020) 15_supplement - p. , 2020
Link:
https://doi.org/10.1212/..
?
10
Development of a Multivariable Proxy Model for Six-Minute W..:
Done, Nicolae
;
Iff, Joel
;
Signorovitch, James
...
Neurology. 94 (2020) 15_supplement - p. , 2020
Link:
https://doi.org/10.1212/..
?
11
Patient and parent oriented tools to assess health-related ..:
Mercuri, Eugenio
;
Messina, Sonia
;
Montes, Jacqueline
...
Neuromuscular Disorders. 30 (2020) 5 - p. 431-436 , 2020
Link:
https://doi.org/10.1016/..
?
12
Disease-specific and glucocorticoid-responsive serum biomar..:
Hathout, Yetrib
;
Liang, Chen
;
Ogundele, Michael
...
Scientific Reports. 9 (2019) 1 - p. , 2019
Link:
https://doi.org/10.1038/..
?
13
Towards regulatory endorsement of drug development tools to..:
the Duchenne Muscular Dystrophy Regulatory Science Consortium (D-RSC)
;
Conrado, Daniela J.
;
Larkindale, Jane
...
Journal of Pharmacokinetics and Pharmacodynamics. 46 (2019) 5 - p. 441-455 , 2019
Link:
https://doi.org/10.1007/..
?
14
Genetic Testing - Muddying the Water for Diagnosis of Infla..:
van de Rijn, Marc
;
Jones, Karra
;
Henricson, Erik
.
Neurology. 92 (2019) 15_supplement - p. , 2019
Link:
https://doi.org/10.1212/..
?
15
Report on the workshop: Meaningful outcome measures for Duc..:
Straub, Volker
;
Mercuri, Eugenio
;
Aartsma-Rus, Annemieke
...
Neuromuscular Disorders. 28 (2018) 8 - p. 690-701 , 2018
Link:
https://doi.org/10.1016/..
1-15