Carelli, Valerio
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10

Indirect Comparison of Lenadogene Nolparvovec Gene Therapy ..:

Carelli, Valerio ; Newman, Nancy J ; Yu-Wai-Man, Patrick...
https://discovery.ucl.ac.uk/id/eprint/10182177/1/Indirect%20Comparison%20of%20Lenadogene%20Nolparvovec%20Gene%20Therapy%20Versus%20Natural%20History%20in%20Patients%20with%20Leber%20Hereditary%20Optic%20Ne.pdf.  , 2023
 
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Efficacy and Safety of Elamipretide in Individuals With Pri..:

Karaa, Amel ; Bertini, Enrico ; Carelli, Valerio...
https://discovery.ucl.ac.uk/id/eprint/10174222/1/e238.full.pdf.  , 2023
 
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