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Clemens, Paula R
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1

Efficacy and Safety of Avalglucosidase Alfa in Patients Wit..:

Kishnani, Priya S ; Diaz-Manera, Jordi ; Toscano, Antonio...
https://scholar.barrowneuro.org/neurology/1471.  , 2023
Link: https://scholar.barrowne..
 
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2

Efficacy and Safety of Viltolarsen in Boys With Duchenne Mu..:

Clemens, Paula R ; Rao, Vamshi K ; Connolly, Anne M...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC10200237/.  , 2023
Link: http://www.ncbi.nlm.nih...
 
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3

Efficacy and Safety of Avalglucosidase Alfa in Patients wit..:

Straub, Volker ; Kostera-Pruszczyk, Anna ; Tammireddy, Swathi...
f6a1c166-a114-4db6-8661-5094b2fca2d6.  , 2023
Link: https://doi.org/10.1001/..
 
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4

Efficacy and Safety of Viltolarsen in Boys With Duchenne Mu..:

Clemens, Paula R ; Rao, Vamishi K ; Connolly, Anne M...
https://orb.binghamton.edu/pharmacy_fac/4.  , 2023
Link: https://orb.binghamton.e..
 
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5

Efficacy and Safety of Avalglucosidase Alfa in Patients Wit..:

Kishnani, Priya S ; Diaz-Manera, Jordi ; Toscano, Antonio...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC10087094/.  , 2023
Link: http://www.ncbi.nlm.nih...
 
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6

Efficacy and Safety of Vamorolone in Duchenne Muscular Dyst..:

Mah, Jean K ; Clemens, Paula R ; Guglieri, Michela...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8790668/.  , 2022
Link: http://www.ncbi.nlm.nih...
 
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7

Efficacy and Safety of Vamorolone in Duchenne Muscular Dyst..:

Mah, Jean K ; Clemens, Paula R ; Guglieri, Michela...
https://discovery.ucl.ac.uk/id/eprint/10142870/1/Ridout_mah_2022_oi_211221_1642537152.18735.pdf.  , 2022
Link: https://discovery.ucl.ac..
 
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8

Safety and efficacy of avalglucosidase alfa versus alglucos..:

Diaz-Manera, Jordi ; Kishnani, Priya S ; Kushlaf, Hani...
https://scholar.barrowneuro.org/neurology/1261.  , 2021
Link: https://scholar.barrowne..
 
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9

Concerns Regarding Therapeutic Implications of Very Low‐Lev..:

Hoffman, Eric P ; Clemens, Paula R
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8251539/.  , 2021
Link: http://www.ncbi.nlm.nih...
 
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10

Multi-Omics Identifies Circulating miRNA and Protein Biomar..:

Heier, Christopher R ; Zhang, Aiping ; Nguyen, Nhu Y...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC7711540/.  , 2020
Link: http://www.ncbi.nlm.nih...
 
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11

The CINRG Becker Natural History Study: Baseline Characteri..:

Clemens, Paula R ; Niizawa, Gabriela ; Feng, Jia...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC7520226/.  , 2020
Link: http://www.ncbi.nlm.nih...
 
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12

Seven-Year Experience From the National Institute of Neurol..:

Cudkowicz, Merit ; Chase, Marianne K ; Coffey, Christopher S...
qt3x83p0r3.  , 2020
Link: https://escholarship.org..
 
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13

Exposure-Response Analysis of Vamorolone (VBP15) in Boys wi..:

Li, Xiaonan ; Conklin, Laurie S ; van den Anker, John...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC7494537/.  , 2020
Link: http://www.ncbi.nlm.nih...
 
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14

Population Pharmacokinetics of Vamorolone (VBP15) in Health..:

Mavroudis, Panteleimon D ; van den Anker, John ; Conklin, Laurie S...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC6548694/.  , 2019
Link: http://www.ncbi.nlm.nih...
 
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15

Vamorolone trial in Duchenne muscular dystrophy shows dose-..:

Hoffman, Eric P ; Schwartz, Benjamin D ; Mengle-Gaw, Laurel J...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC7011869/.  , 2019
Link: http://www.ncbi.nlm.nih...
 
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