Aiach, Karen
13  results:
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1

Focal lesions following intracerebral gene therapy for muco..:

Bugiani, Marianna ; Abbink, Truus E. M. ; Edridge, Arthur W. D....
Annals of Clinical and Translational Neurology.  10 (2023)  6 - p. 904-917 , 2023
 
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2

An observational, prospective, multicenter, natural history..:

Wijburg, Frits A. ; Aiach, Karen ; Chakrapani, Anupam...
Molecular Genetics and Metabolism.  135 (2022)  2 - p. 133-142 , 2022
 
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4

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy - Methods & Clinical Development.  27 (2022)  - p. 281-292 , 2022
 
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9

An observational, prospective, multicenter, natural history..:

Wijburg, Frits ; Aiach, Karen ; Chakrapani, Anupam...
Molecular genetics and metabolism. Amsterdam. Vol. 135 (2022), p. 133-142..  , 2022
 
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13

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Michaël Hocquemiller ; Laura Giersch ; Xin Mei...
http://www.sciencedirect.com/science/article/pii/S2329050122001462.  , 2022
 
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