Bangari, Dinesh S.
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Anti-human-TfR-GAA efficiently clears CNS and muscle glycog..:

van der Flier, Arjan ; Riley, Raquel ; Smith, Laurie...
Molecular Genetics and Metabolism.  141 (2024)  2 - p. 108062 , 2024
 
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AAV-ARSA-mediated gene replacement for the treatment of met..:

Ramachandran, Shyam ; Ardinger, Jeffery ; Bu, Jie...
Molecular Genetics and Metabolism.  138 (2023)  2 - p. 107284 , 2023
 
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