E-LIB Suche - Ergebnisse für: Childers, Martin K.

1

Safety and efficacy of gene replacement therapy for X-linke..:

Shieh, Perry B ; Kuntz, Nancy L ; Dowling, James J...
The Lancet Neurology. 22 (2023) 12 - p. 1125-1139 , 2023

Link: https://doi.org/10.1016/..

2

Increased tissue stiffness triggers contractile dysfunction..:

Chang, Alex C.Y. ; Pardon, Gaspard ; Chang, Andrew C.H....
Stem Cell Reports. 16 (2021) 9 - p. 2169-2181 , 2021

Link: https://doi.org/10.1016/..

3

AAV-Mediated Gene Transfer Restores a Normal Muscle Transcr..:

Dupont, Jean-Baptiste ; Guo, Jianjun ; Renaud-Gabardos, Edith...
Molecular Therapy. 28 (2020) 2 - p. 382-393 , 2020

Link: https://doi.org/10.1016/..

4

A phase 1 study of gene therapy with ACTUS-101 in late-onse..:

Koeberl, Dwight ; Smith, Edward C. ; Case, Laura E....
Molecular Genetics and Metabolism. 129 (2020) 2 - p. S91 , 2020

Link: https://doi.org/10.1016/..

5

Gene Therapy for X-Linked Myotubular Myopathy:

, In: Muscle Gene Therapy,

Dupont, Jean-Baptiste ; Lawlor, Michael W. ; Childers, Martin K. - p. 565-577 , 2019

Link: https://doi.org/10.1007/..

6

Absence of full-length dystrophin impairs normal maturation..:

Pioner, J Manuel ; Guan, Xuan ; Klaiman, Jordan M...
Cardiovascular Research. 116 (2019) 2 - p. 368-382 , 2019

Link: https://doi.org/10.1093/..

7

Histological and Biochemical Evaluation of Muscle Gene Ther..:

, In: Muscle Gene Therapy,

Lawlor, Michael W. ; Schneider, Joel S. ; Childers, Martin K.. - p. 207-226 , 2019

Link: https://doi.org/10.1007/..

8

Exosome-Mediated Benefits of Cell Therapy in Mouse and Huma..:

Aminzadeh, Mark A. ; Rogers, Russell G. ; Fournier, Mario...
Stem Cell Reports. 10 (2018) 3 - p. 942-955 , 2018

Link: https://doi.org/10.1016/..

9

Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Corre..:

Mack, David L. ; Poulard, Karine ; Goddard, Melissa A....
Molecular Therapy. 25 (2017) 4 - p. 839-854 , 2017

Link: https://doi.org/10.1016/..

10

Isolation and characterization of canine perivascular stem/..:

James, Aaron W. ; Zhang, Xinli ; Crisan, Mihaela...
PLOS ONE. 12 (2017) 5 - p. e0177308 , 2017

Link: https://doi.org/10.1371/..

11

Cardiac involvement in female carriers of Duchenne or Becke..:

Childers, Martin K. ; Klaiman, Jordan M.
Muscle & Nerve. 55 (2017) 6 - p. 777-779 , 2017

Link: https://doi.org/10.1002/..

12

Long‐term effects of systemic gene therapy in a canine mode..:

Elverman, Matthew ; Goddard, Melissa A. ; Mack, David...
Muscle & Nerve. 56 (2017) 5 - p. 943-953 , 2017

Link: https://doi.org/10.1002/..

13

Isolation and Mechanical Measurements of Myofibrils from Hu..:

Pioner, Josè Manuel ; Racca, Alice W. ; Klaiman, Jordan M....
Stem Cell Reports. 6 (2016) 6 - p. 885-896 , 2016

Link: https://doi.org/10.1016/..

14

Skeletal Muscle Pathology in X-Linked Myotubular Myopathy: ..:

Lawlor, Michael W. ; Beggs, Alan H. ; Buj-Bello, Ana...
Journal of Neuropathology & Experimental Neurology. 75 (2016) 2 - p. 102-110 , 2016

Link: https://doi.org/10.1093/..

15

Gene therapy in monogenic congenital myopathies:

Guan, Xuan ; Goddard, Melissa A. ; Mack, David L..
Methods. 99 (2016) - p. 91-98 , 2016

Link: https://doi.org/10.1016/..