Droege, M.
~ 200  results:
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2

SMA - CLINICAL:

Droege, M. ; Dabbous, O. ; Arjunji, R....
Neuromuscular Disorders.  30 (2020)  - p. S70 , 2020
 
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4

SMA: REGISTRIES, BIOMARKERS & OUTCOME MEASURES:

Servais, L. ; Day, J. ; De Vivo, D....
Neuromuscular Disorders.  30 (2020)  - p. S97 , 2020
 
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5

SMA – THERAPY:

Dabbous, O. ; Reyna, S. ; Feltner, D....
Neuromuscular Disorders.  30 (2020)  - p. S123 , 2020
 
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6

PND13 Burden of Illness of Spinal Muscular Atrophy: An Upda..:

Droege, M. ; Dabbous, O. ; Arjunji, R....
Value in Health Regional Issues.  22 (2020)  - p. S76-S77 , 2020
 
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7

REGISTRIES:

Servais, L. ; Day, J. ; De Vivo, D....
Neuromuscular Disorders.  29 (2019)  - p. S195 , 2019
 
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9

Burden of illness of spinal muscular atrophy type 1 (SMA1):

Droege, M. ; Dabbous, O. ; Arjunji, R....
Journal of the Neurological Sciences.  405 (2019)  - p. 58 , 2019
 
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10

P.357Type I spinal muscular atrophy patients treated with A..:

Arjunji, R. ; Dean, R. ; Jensen, I....
Neuromuscular Disorders.  29 (2019)  - p. S185-S186 , 2019
 
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11

P.062 Burden of illness of spinal muscular atrophy (SMA): a..:

Droege, M ; Dabbous, O ; Arjunji, R...
Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques.  46 (2019)  s1 - p. S30-S31 , 2019
 
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12

PND18 THE RESTORE REGISTRY: A RESOURCE FOR MEASURING AND IM..:

Servais, L. ; Day, J.W. ; De Vivo, D.C....
Value in Health Regional Issues.  19 (2019)  - p. S62 , 2019
 
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14

PBI1 THE VALUE OF ONASEMNOGENE ABEPARVOVEC (AVXS-101) AS A ..:

Malone, D.C. ; Arjunji, R. ; Dean, R....
Value in Health Regional Issues.  19 (2019)  - p. S11 , 2019
 
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15

P.061 The value of AVXS-101 gene-replacement therapy for Sp..:

Dabbous, O ; Sproule, DM ; Feltner, DE...
Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques.  46 (2019)  s1 - p. S30 , 2019
 
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