E-LIB Suche - Ergebnisse für: Harrison, Patrick T.

1

Correction: Cost of gene therapy:

Harrison, Patrick T. ; Friedmann, Theodore
Gene Therapy. , 2024

Link: https://doi.org/10.1038/..

2

Development of novel therapeutics for all individuals with ..:

Amaral, Margarida D. ; Harrison, Patrick T.
Journal of Cystic Fibrosis. 22 (2023) - p. S45-S49 , 2023

Link: https://doi.org/10.1016/..

3

Use of adenine base editing and homology-independent target..:

Mention, Karen ; Cavusoglu-Doran, Kader ; Joynt, Anya T...
Human Molecular Genetics. 32 (2023) 23 - p. 3237-3248 , 2023

Link: https://doi.org/10.1093/..

4

Mutation-class dependent signatures outweigh disease-associ..:

Santos, Lúcia ; Nascimento, Rui ; Duarte, Aires...
Cell & Bioscience. 13 (2023) 1 - p. , 2023

Link: https://doi.org/10.1186/..

5

Molecular and functional correction of a deep intronic spli..:

Walker, Amy J. ; Graham, Carina ; Greenwood, Miriam...
Molecular Therapy - Methods & Clinical Development. 31 (2023) - p. 101140 , 2023

Link: https://doi.org/10.1016/..

6

Cost of gene therapy:

Harrison, Patrick T. ; Friedmann, Theodore
Gene Therapy. 30 (2023) 10-11 - p. 737-737 , 2023

Link: https://doi.org/10.1038/..

7

CFTR RNA- and DNA-based therapies:

Harrison, Patrick T.
Current Opinion in Pharmacology. 65 (2022) - p. 102247 , 2022

Link: https://doi.org/10.1016/..

8

Comparison of Cas9 and Cas12a CRISPR editing methods to cor..:

Santos, Lúcia ; Mention, Karen ; Cavusoglu-Doran, Kader...
Journal of Cystic Fibrosis. 21 (2022) 1 - p. 181-187 , 2022

Link: https://doi.org/10.1016/..

9

Prime editing – an update on the field:

Scholefield, Janine ; Harrison, Patrick T.
Gene Therapy. 28 (2021) 7-8 - p. 396-401 , 2021

Link: https://doi.org/10.1038/..

10

In Vitro and In Vivo Models to Study Nephropathic Cystinosi:

Cheung, Pang Yuk ; Harrison, Patrick T. ; Davidson, Alan J..
Cells. 11 (2021) 1 - p. 6 , 2021

Link: https://doi.org/10.3390/..

11

CRISPR Deletion of a SVA Retrotransposon Demonstrates Funct..:

Price, Emma ; Gianfrancesco, Olympia ; Harrison, Patrick T....
International Journal of Molecular Sciences. 22 (2021) 4 - p. 1911 , 2021

Link: https://doi.org/10.3390/..

12

Polycystic Kidney Disease Ryanodine Receptor Domain (PKDRR)..:

Zheng, Limian ; Prestwich, Barbara Doyle ; Harrison, Patrick T..
Pathogens. 9 (2020) 7 - p. 577 , 2020

Link: https://doi.org/10.3390/..

13

Gene and Base Editing as a Therapeutic Option for Cystic Fi..:

Mention, Karen ; Santos, Lúcia ; Harrison, Patrick T.
Genes. 10 (2019) 5 - p. 387 , 2019

Link: https://doi.org/10.3390/..

14

The Regulation of Monoamine Oxidase A Gene Expression by Di..:

Manca, Maurizio ; Pessoa, Veridiana ; Lopez, Ana Illera...
Journal of Molecular Neuroscience. 64 (2018) 3 - p. 459-470 , 2018

Link: https://doi.org/10.1007/..

15

A beginner's guide to gene editing:

Harrison, Patrick T. ; Hart, Stephen
Experimental Physiology. 103 (2018) 4 - p. 439-448 , 2018

Link: https://doi.org/10.1113/..