E-LIB Suche - Ergebnisse für: Kuntz, N.

1

P210 Interim results from the RESPOND study evaluating nusi..:

Parsons, J. ; Kuntz, N. ; Brandsema, J....
Neuromuscular Disorders. 33 (2023) - p. S87 , 2023

Link: https://doi.org/10.1016/..

2

P01 Risdiplam experience following onasemnogene abeparvovec..:

Kuntz, N. ; Svoboda, M. ; Leon-Astudillo, C....
Neuromuscular Disorders. 33 (2023) - p. S162 , 2023

Link: https://doi.org/10.1016/..

3

P.14 Analysis of the longitudinal CINRG Becker natural hist..:

Clemens, P. ; Gordish-Dressman, H. ; Niizawa, G....
Neuromuscular Disorders. 32 (2022) - p. S50 , 2022

Link: https://doi.org/10.1016/..

4

O.06 Long term outcomes for X-Linked myotubular Myopathy (X..:

Shieh, P. ; Kuntz, N. ; Dowling, J....
Neuromuscular Disorders. 32 (2022) - p. S44 , 2022

Link: https://doi.org/10.1016/..

5

P.100 Rationale/design of the phase 3b ASCEND study of inve..:

Darras, B. ; Hagenacker, T. ; Finkel, R....
Neuromuscular Disorders. 32 (2022) - p. S86 , 2022

Link: https://doi.org/10.1016/..

6

CLINICAL TRIAL HIGHLIGHTS:

Hoffman, E. ; Dang, U. ; Clemens, P....
Neuromuscular Disorders. 31 (2021) - p. S48 , 2021

Link: https://doi.org/10.1016/..

7

CLINICAL TRIAL HIGHLIGHTS:

Shieh, P. ; Kuntz, N. ; Dowling, J....
Neuromuscular Disorders. 31 (2021) - p. S47 , 2021

Link: https://doi.org/10.1016/..

8

DMD - TREATMENT:

Hoffman, E. ; Dang, U. ; Clemens, P....
Neuromuscular Disorders. 31 (2021) - p. S93-S94 , 2021

Link: https://doi.org/10.1016/..

9

REGISTRIES, CARE, QUALITY OF LIFE, MANAGEMENT OF NMD:

Brown, L. ; Hoffman, K. ; Krosschell, K....
Neuromuscular Disorders. 30 (2020) - p. S145-S146 , 2020

Link: https://doi.org/10.1016/..

10

SMA: REGISTRIES, BIOMARKERS & OUTCOME MEASURES:

Krosschell, K. ; Brown, L. ; Hoffman, K....
Neuromuscular Disorders. 30 (2020) - p. S98 , 2020

Link: https://doi.org/10.1016/..

11

DMD – THERAPY:

Kuntz, N. ; Wagner, K. ; East, L....
Neuromuscular Disorders. 30 (2020) - p. S130-S131 , 2020

Link: https://doi.org/10.1016/..

12

SMA – THERAPY:

Mercuri, E. ; Darras, B. ; Chiriboga, C....
Neuromuscular Disorders. 30 (2020) - p. S121 , 2020

Link: https://doi.org/10.1016/..

13

MUSCLE FUNCTION & HOMEOSTASIS / MOLECULAR THERAPEUTIC APPRO..:

Shieh, P. ; Kuntz, N. ; Bönnemann, C....
Neuromuscular Disorders. 30 (2020) - p. S65-S66 , 2020

Link: https://doi.org/10.1016/..

14

SMA – THERAPY:

Chand, D. ; Finkel, R. ; Day, J....
Neuromuscular Disorders. 30 (2020) - p. S120 , 2020

Link: https://doi.org/10.1016/..

15

P.105INCEPTUS pre-phase 1, prospective, non-interventional,..:

Servais, L. ; Shieh, P. ; Dowling, J....
Neuromuscular Disorders. 29 (2019) - p. S79 , 2019

Link: https://doi.org/10.1016/..