E-LIB Suche - Ergebnisse für: Lu, Qi Long

1

Improved efficacy of FKRP AAV gene therapy by combination w..:

Cataldi, Marcela P. ; Vannoy, Charles H. ; Blaeser, Anthony...
Molecular Therapy. 31 (2023) 12 - p. 3478-3489 , 2023

Link: https://doi.org/10.1016/..

2

Ribitol dose-dependently enhances matriglycan expression an..:

Wu, Bo ; Drains, Morgan ; Shah, Sapana N....
PLOS ONE. 17 (2022) 12 - p. e0278482 , 2022

Link: https://doi.org/10.1371/..

3

Ribitol alters multiple metabolic pathways of central carbo..:

Tucker, Jason Driver ; Doddapaneni, Ravi ; Lu, Pei Juan..
PLOS ONE. 17 (2022) 12 - p. e0278711 , 2022

Link: https://doi.org/10.1371/..

4

Revertant Phenomenon in DMD and LGMD2I and Its Therapeutic ..:

Lu, Qi Long ; Jaiswal, Jyoti ; Nagaraju, Kanneboyina
Journal of Neuromuscular Diseases. 8 (2021) s2 - p. S359-S367 , 2021

Link: https://doi.org/10.3233/..

5

A universal gene correction approach for FKRP-associated dy..:

Dhoke, Neha R. ; Kim, Hyunkee ; Selvaraj, Sridhar...
Cell Reports. 36 (2021) 2 - p. 109360 , 2021

Link: https://doi.org/10.1016/..

6

Efficient engraftment of pluripotent stem cell-derived myog..:

Azzag, Karim ; Ortiz-Cordero, Carolina ; Oliveira, Nelio A. J....
Skeletal Muscle. 10 (2020) 1 - p. , 2020

Link: https://doi.org/10.1186/..

7

ISPD Overexpression Enhances Ribitol-Induced Glycosylation ..:

Cataldi, Marcela P. ; Blaeser, Anthony ; Lu, Peijuan..
Molecular Therapy - Methods & Clinical Development. 17 (2020) - p. 271-280 , 2020

Link: https://doi.org/10.1016/..

8

Metabolomics Analysis of Skeletal Muscles from FKRP-Deficie..:

Vannoy, Charles Harvey ; Leroy, Victoria ; Broniowska, Katarzyna.
Scientific Reports. 9 (2019) 1 - p. , 2019

Link: https://doi.org/10.1038/..

9

Dose-Dependent Effects of FKRP Gene-Replacement Therapy on ..:

Vannoy, Charles Harvey ; Leroy, Victoria ; Lu, Qi Long
Molecular Therapy - Methods & Clinical Development. 11 (2018) - p. 106-120 , 2018

Link: https://doi.org/10.1016/..

10

Ribitol restores functionally glycosylated α-dystroglycan a..:

Cataldi, Marcela P. ; Lu, Peijuan ; Blaeser, Anthony.
Nature Communications. 9 (2018) 1 - p. , 2018

Link: https://doi.org/10.1038/..

11

Efficacy of Gene Therapy Is Dependent on Disease Progressio..:

Vannoy, Charles Harvey ; Xiao, Will ; Lu, Peijuan..
Molecular Therapy - Methods & Clinical Development. 5 (2017) - p. 31-42 , 2017

Link: https://doi.org/10.1016/..

12

Elusive sources of variability of dystrophin rescue by exon..:

Vila, Maria Candida ; Klimek, Margaret Benny ; Novak, James S....
Skeletal Muscle. 5 (2015) 1 - p. , 2015

Link: https://doi.org/10.1186/..

13

Mouse models of fukutin-related protein mutations show a wi..:

Blaeser, Anthony ; Keramaris, Elizabeth ; Chan, Yiumo M....
Human Genetics. 132 (2013) 8 - p. 923-934 , 2013

Link: https://doi.org/10.1007/..

14

Adeno-associated Virus 9 Mediated FKRP Gene Therapy Restore..:

Xu, Lei ; Lu, Pei Juan ; Wang, Chi-Hsien...
Molecular Therapy. 21 (2013) 10 - p. 1832-1840 , 2013

Link: https://doi.org/10.1038/..

15

Long-Term Rescue of Dystrophin Expression and Improvement i..:

Wu, Bo ; Lu, Peijuan ; Cloer, Caryn...
The American Journal of Pathology. 181 (2012) 2 - p. 392-400 , 2012

Link: https://doi.org/10.1016/..