E-LIB Suche - Ergebnisse für: Mollin, Anna

1

Preclinical Studies of Gene Replacement Therapy for CDKL5 D..:

Voronin, Gregory ; Narasimhan, Jana ; Gittens, Jamila...
Molecular Therapy. , 2024

Link: https://doi.org/10.1016/..

2

Evaluation of the Biodistribution, Efficacy, and Side-Effec..:

Liu, Grace ; Lipari, Phil ; Mollin, Anna...
Neurology. 100 (2023) 17_supplement_2 - p. , 2023

Link: https://doi.org/10.1212/..

3

Development of an oral treatment that rescues gait ataxia a..:

Morini, Elisabetta ; Chekuri, Anil ; Logan, Emily M....
The American Journal of Human Genetics. 110 (2023) 3 - p. 531-547 , 2023

Link: https://doi.org/10.1016/..

4

Comparison of pharmaceutical properties and biological acti..:

Liu, Grace ; Lipari, Philip ; Mollin, Anna...
Human Molecular Genetics. 33 (2023) 3 - p. 211-223 , 2023

Link: https://doi.org/10.1093/..

5

Emvododstat, a Potent Dihydroorotate Dehydrogenase Inhibito..:

Branstrom, Arthur ; Cao, Liangxian ; Furia, Bansri...
Frontiers in Oncology. 12 (2022) - p. , 2022

Link: https://doi.org/10.3389/..

6

Quantitation of Pax-6 protein in ocular impression cytology..:

Zaworski, Phillip G. ; Schwartz, Rachel ; Burr, Jeffrey...
Analytical Biochemistry. 656 (2022) - p. 114876 , 2022

Link: https://doi.org/10.1016/..

7

Preclinical and Early Clinical Development of PTC596, a Nov..:

Jernigan, Finith ; Branstrom, Arthur ; Baird, John D....
Molecular Cancer Therapeutics. 20 (2021) 10 - p. 1846-1857 , 2021

Link: https://doi.org/10.1158/..

8

SMN protein is required throughout life to prevent spinal m..:

Zhao, Xin ; Feng, Zhihua ; Risher, Nicole...
Human Molecular Genetics. 31 (2021) 1 - p. 82-96 , 2021

Link: https://doi.org/10.1093/..

9

Chemical modifications of G418 (geneticin): Synthesis of no..:

Baiazitov, Ramil Y. ; Friesen, Westley ; Johnson, Briana...
Carbohydrate Research. 495 (2020) - p. 108058 , 2020

Link: https://doi.org/10.1016/..

10

The minor gentamicin complex component, X2, is a potent pre..:

Friesen, Westley J. ; Johnson, Briana ; Sierra, Jairo...
PLOS ONE. 13 (2018) 10 - p. e0206158 , 2018

Link: https://doi.org/10.1371/..

11

Pharmacokinetics, pharmacodynamics, and efficacy of a small..:

Zhao, Xin ; Feng, Zhihua ; Ling, Karen K. Y....
Human Molecular Genetics. 25 (2016) 10 - p. 1885-1899 , 2016

Link: https://doi.org/10.1093/..

12

Structure–Activity Relationship (SAR) Optimization of 6-(In..:

Zhang, Nanjing ; Zhang, Xiaoyan ; Zhu, Jin...
Journal of Medicinal Chemistry. 57 (2013) 5 - p. 2121-2135 , 2013

Link: https://doi.org/10.1021/..

13

PTC124 targets genetic disorders caused by nonsense mutatio..:

Welch, Ellen M. ; Barton, Elisabeth R. ; Zhuo, Jin...
Nature. 447 (2007) 7140 - p. 87-91 , 2007

Link: https://doi.org/10.1038/..

14

Development of an oral treatment that rescues gait ataxia a..:

Morini, Elisabetta ; Chekuri, Anil ; Logan, Emily M...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC10027479/. , 2023

Link: http://www.ncbi.nlm.nih...

15

Emvododstat, a Potent Dihydroorotate Dehydrogenase Inhibito..:

Branstrom, Arthur ; Cao, Liangxian ; Furia, Bansri...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8864546/. , 2022

Link: http://www.ncbi.nlm.nih...