Proud, Crystal
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12

Real-World Outcomes in Patients with Spinal Muscular Atroph..:

Servais, Laurent ; Day, John W. ; De Vivo, Darryl C....
Journal of Neuromuscular Diseases.  11 (2024)  2 - p. 425-442 , 2024
 
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14

Combination disease‐modifying treatment in spinal muscular ..:

Proud, Crystal M. ; Mercuri, Eugenio ; Finkel, Richard S....
Annals of Clinical and Translational Neurology.  10 (2023)  11 - p. 2155-2160 , 2023
 
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