Sena de Miranda, Michael Douglas
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Contributors:

, In: Huntington's Disease,
 
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5

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy - Methods & Clinical Development.  27 (2022)  - p. 281-292 , 2022
 
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6

Real-time MR tracking of AAV gene therapy with βgal-respons..:

Taghian, Toloo ; Batista, Ana Rita ; Kamper, Sarah...
Molecular Therapy - Methods & Clinical Development.  23 (2021)  - p. 128-134 , 2021
 
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