I agree that this site is using cookies. You can find further informations here.
X
Sena-Esteves, Miguel
466  results:
Search for persons X
?
1

Adeno-associated viral gene therapy for sialidosis using sm..:

Gallagher, Jillian ; Gallant, Judith ; Xu, Ping...
Molecular Genetics and Metabolism.  141 (2024)  2 - p. 107834 , 2024
Link: https://doi.org/10.1016/..
 
?
2

EZH2 inhibition reactivates epigenetically silenced FMR1 an..:

Fang, Minggang ; Deibler, Sara K. ; Krishnamurthy, Pranathi Meda...
Frontiers in Neuroscience.  18 (2024)  - p. , 2024
Link: https://doi.org/10.3389/..
 
?
3

Expression of ALS-PFN1 impairs vesicular degradation in iPS..:

Funes, Salome ; Jung, Jonathan ; Gadd, Del Hayden...
Nature Communications.  15 (2024)  1 - p. , 2024
Link: https://doi.org/10.1038/..
 
?
4

Contributors:

, In: Huntington's Disease,
Aaronson, Jeffrey S. ; Abramovich, Juliana ; Aronin, Neil... - p. xiii-xvi , 2024
Link: https://doi.org/10.1016/..
 
?
5

Focused Ultrasound-Mediated Disruption of the Blood–Brain B..:

Owusu-Yaw, Bernie S. ; Zhang, Yongzhi ; Garrett, Lilyan...
Pharmaceutics.  16 (2024)  6 - p. 710 , 2024
Link: https://doi.org/10.3390/..
 
?
6

Huntingtin lowering therapeutics:

, In: Huntington's Disease,
Aronin, Neil ; Sena-Esteves, Miguel ; Khvorova, Anastasia.. - p. 523-549 , 2024
Link: https://doi.org/10.1016/..
 
?
7

Awake intracerebroventricular delivery and safety assessmen..:

Benatti, Hector Ribeiro ; Prestigiacomo, Rachel D. ; Taghian, Toloo...
Molecular Therapy - Methods & Clinical Development.  31 (2023)  - p. 101122 , 2023
Link: https://doi.org/10.1016/..
 
?
8

From mouse to sheep: Generating a sheep model and developin..:

Gallagher, Jillian ; Gallant, Judith ; Xu, Ping...
Molecular Genetics and Metabolism.  138 (2023)  2 - p. 107109 , 2023
Link: https://doi.org/10.1016/..
 
?
9

DIPG-17. TREATMENT OF DIFFUSE INTRINSIC PONTINE GLIOMA USIN..:

Wentworth, Simon ; Batista, Ana Rita ; Alterman, Julia..
Neuro-Oncology.  25 (2023)  Supplement_1 - p. i16-i16 , 2023
Link: https://doi.org/10.1093/..
 
?
10

AAV gene therapy for Tay-Sachs disease:

Flotte, Terence R. ; Cataltepe, Oguz ; Puri, Ajit...
Nature Medicine.  28 (2022)  2 - p. 251-259 , 2022
Link: https://doi.org/10.1038/..
 
?
11

OR18-1 The Impact of Makorin Ring Finger Protein 3 (MKRN3) ..:

Carroll, Rona ; Kaiser, Ursula ; Kim, Han Kyeol...
Journal of the Endocrine Society.  6 (2022)  Supplement_1 - p. A616-A617 , 2022
Link: https://doi.org/10.1210/..
 
?
12

Anti-SOD1 Nanobodies That Stabilize Misfolded SOD1 Proteins..:

Kumar, Meenakshi Sundaram ; Fowler-Magaw, Megan E. ; Kulick, Daniel...
International Journal of Molecular Sciences.  23 (2022)  24 - p. 16013 , 2022
Link: https://doi.org/10.3390/..
 
?
13

AAVrh10 vector corrects pathology in animal models of GM1 g..:

Hocquemiller, Michaël ; Giersch, Laura ; Mei, Xin...
Molecular Therapy - Methods & Clinical Development.  27 (2022)  - p. 281-292 , 2022
Link: https://doi.org/10.1016/..
 
?
14

Sialidosis: From gene editing to gene therapy:

Gallagher, Jillian ; Gallant, Judith ; Xu, Ping...
Molecular Genetics and Metabolism.  135 (2022)  2 - p. S45 , 2022
Link: https://doi.org/10.1016/..
 
?
15

Natural history of Tay-Sachs disease in sheep:

Story, Brett ; Taghian, Toloo ; Gallagher, Jillian...
Molecular Genetics and Metabolism.  134 (2021)  1-2 - p. 164-174 , 2021
Link: https://doi.org/10.1016/..
 
1-15