Simmons, Tabatha
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5

Systemic delivery of an AAV9 exon-skipping vector significa..:

Wein, Nicolas ; Vetter, Tatyana A. ; Vulin, Adeline...
Molecular Therapy - Methods & Clinical Development.  26 (2022)  - p. 279-293 , 2022
 
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6

A first-in-human phase I/IIa gene transfer clinical trial f..:

Flanigan, Kevin M. ; Vetter, Tatyana A. ; Simmons, Tabatha R....
Molecular Therapy - Methods & Clinical Development.  27 (2022)  - p. 47-60 , 2022
 
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8

Pre-clinical dose-escalation studies establish a therapeuti..:

Simmons, Tabatha R. ; Vetter, Tatyana A. ; Huang, Nianyuan...
Molecular Therapy - Methods & Clinical Development.  21 (2021)  - p. 325-340 , 2021
 
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