E-LIB Suche - Ergebnisse für: Srifa, Waracharee

1

Gene replacement of α-globin with β-globin restores hemoglo..:

Cromer, M. Kyle ; Camarena, Joab ; Martin, Renata M....
Nature Medicine. 27 (2021) 4 - p. 677-687 , 2021

Link: https://doi.org/10.1038/..

2

Cas9-AAV6-engineered human mesenchymal stromal cells improv..:

Srifa, Waracharee ; Kosaric, Nina ; Amorin, Alvaro...
Nature Communications. 11 (2020) 1 - p. , 2020

Link: https://doi.org/10.1038/..

3

Macrophage Subpopulation Dynamics Shift following Intraveno..:

Kosaric, Nina ; Srifa, Waracharee ; Bonham, Clark A....
Molecular Therapy. 28 (2020) 9 - p. 2007-2022 , 2020

Link: https://doi.org/10.1016/..

4

Metabolic engineering generates a transgene-free safety swi..:

Wiebking, Volker ; Patterson, James O. ; Martin, Renata...
Nature Biotechnology. 38 (2020) 12 - p. 1441-1450 , 2020

Link: https://doi.org/10.1038/..

5

Author Correction: Gene correction for SCID-X1 in long-term..:

Pavel-Dinu, Mara ; Wiebking, Volker ; Dejene, Beruh T....
Nature Communications. 10 (2019) 1 - p. , 2019

Link: https://doi.org/10.1038/..

6

Author Correction: Gene correction for SCID-X1 in long-term..:

Pavel-Dinu, Mara ; Wiebking, Volker ; Dejene, Beruh T....
Nature Communications. 10 (2019) 1 - p. , 2019

Link: https://doi.org/10.1038/..

7

Highly efficient editing of the β-globin gene in patient-de..:

Park, So Hyun ; Lee, Ciaran M ; Dever, Daniel P...
Nucleic Acids Research. 47 (2019) 15 - p. 7955-7972 , 2019

Link: https://doi.org/10.1093/..

8

Gene correction for SCID-X1 in long-term hematopoietic stem..:

Pavel-Dinu, Mara ; Wiebking, Volker ; Dejene, Beruh T....
Nature Communications. 10 (2019) 1 - p. , 2019

Link: https://doi.org/10.1038/..

9

Rapid Phenotypic and Genotypic Diversification After Exposu..:

Forche, Anja ; Cromie, Gareth ; Gerstein, Aleeza C...
Genetics. 209 (2018) 3 - p. 725-741 , 2018

Link: https://doi.org/10.1534/..

10

Precise Correction of Disease Mutations in Induced Pluripot..:

Turan, Soeren ; Farruggio, Alfonso P ; Srifa, Waracharee..
Molecular Therapy. 24 (2016) 4 - p. 685-696 , 2016

Link: https://doi.org/10.1038/..

11

Gene replacement of α-globin with β-globin restores hemoglo..:

Cromer, M. Kyle ; Camarena, Joab ; Martin, Renata M...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8265212/. , 2021

Link: http://www.ncbi.nlm.nih...

12

Development of β-globin gene correction in human hematopoie..:

Lattanzi, Annalisa ; Camarena, Joab ; Lahiri, Premanjali...
Lattanzi , A , Camarena , J , Lahiri , P , Segal , H , Srifa , W , Vakulskas , C A , Frock , R L , Kenrick , J , Lee , C , Talbott , N , Skowronski , J , Cromer , M K , Charlesworth , C T , Bak , R O , Mantri , S , Bao , G , DiGiusto , D , Tisdale , J , Wright , J F , Bhatia , N , Roncarolo , M G , Dever , D P & Porteus , M H 2021 , ' Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease ' , Science Translational Medicine , vol. 13 , no. 598 , eabf2444 . https://doi.org/10.1126/scitranslmed.abf2444. , 2021

Link: https://pure.au.dk/porta..

13

Development of β-globin gene correction in human hematopoie..:

Lattanzi, Annalisa ; Camarena, Joab ; Lahiri, Premanjali...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8862191/. , 2021

Link: http://www.ncbi.nlm.nih...

14

Gene replacement of α-globin with β-globin restores hemoglo..:

Cromer, M Kyle ; Camarena, Joab ; Martin, Renata M...
Cromer , M K , Camarena , J , Martin , R M , Lesch , B J , Vakulskas , C A , Bode , N M , Kurgan , G , Collingwood , M A , Rettig , G R , Behlke , M A , Lemgart , V T , Zhang , Y , Goyal , A , Zhao , F , Ponce , E , Srifa , W , Bak , R O , Uchida , N , Majeti , R , Sheehan , V A , Tisdale , J F , Dever , D P & Porteus , M H 2021 , ' Gene replacement of α-globin with β-globin restores hemoglobin balance in β-thalassemia-derived hematopoietic stem and progenitor cells ' , Nature Medicine , vol. 27 , no. 4 , pp. 677-687 . https://doi.org/10.1038/s41591-021-01284-y. , 2021

Link: https://pure.au.dk/porta..

15

Macrophage Subpopulation Dynamics Shift following Intraveno..:

Kosaric, Nina ; Srifa, Waracharee ; Bonham, Clark A...
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC7474342/. , 2020

Link: http://www.ncbi.nlm.nih...