Wein, N.
309  results:
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2

P14 U7snRNA-mediated exon skipping as a powerful therapeuti..:

Saylam, E. ; Terry, K. ; Suhaiba, A....
Neuromuscular Disorders.  33 (2023)  - p. S100-S101 , 2023
 
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3

DMD - TREATMENT:

Gushchina, L. ; Bradley, A. ; Vetter, T....
Neuromuscular Disorders.  31 (2021)  - p. S93 , 2021
 
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4

DMD – ANIMAL MODELS & PRECLINICAL TREATMENT:

Gushchina, L. ; Frair, E. ; Rohan, N....
Neuromuscular Disorders.  30 (2020)  - p. S109 , 2020
 
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5

DMD – ANIMAL MODELS & PRECLINICAL TREATMENT:

Wein, N. ; Simmons, T. ; Rajakumar, D....
Neuromuscular Disorders.  30 (2020)  - p. S107 , 2020
 
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6

DMD – ANIMAL MODELS & PRECLINICAL TREATMENT:

Gushchina, L. ; Grounds, K. ; Frair, E....
Neuromuscular Disorders.  30 (2020)  - p. S108-S109 , 2020
 
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10

A single neonatal delivery of an exon 2 directed AAV9.U7snR..:

Wein, N. ; Simmons, T. ; Gumienny, F....
Neuromuscular Disorders.  26 (2016)  - p. S126-S127 , 2016
 
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11

Early expression of ΔCH1 dystrophin isoform reverses or pre..:

Wein, N. ; Vulin, A. ; Simmons, T....
Neuromuscular Disorders.  25 (2015)  - p. S292-S293 , 2015
 
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12

G.P.96:

Simmons, T. ; Wein, N. ; Vulin-Chaffiol, A....
Neuromuscular Disorders.  24 (2014)  9-10 - p. 823-824 , 2014
 
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13

G.P.94:

Wein, N. ; Vulin, A. ; Simmons, T....
Neuromuscular Disorders.  24 (2014)  9-10 - p. 823 , 2014
 
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