I agree that this site is using cookies. You can find further informations here.
X
Wein, Nicolas
133  results:
Search for persons X
?
1

Persistence of exon 2 skipping and dystrophin expression at..:

Gushchina, Liubov V. ; Bradley, Adrienne J. ; Vetter, Tatyana A....
Molecular Therapy - Methods & Clinical Development.  31 (2023)  - p. 101144 , 2023
Link: https://doi.org/10.1016/..
 
?
2

Neuron-Schwann cell interactions in peripheral nervous syst..:

Oliveira, Julia Teixeira ; Yanick, Christopher ; Wein, Nicolas.
Frontiers in Cellular Neuroscience.  17 (2023)  - p. , 2023
Link: https://doi.org/10.3389/..
 
?
3

Novel MECP2 gene therapy is effective in a multicenter stud..:

Powers, Samantha ; Likhite, Shibi ; Gadalla, Kamal K....
Molecular Therapy.  31 (2023)  9 - p. 2767-2782 , 2023
Link: https://doi.org/10.1016/..
 
?
4

Promising AAV.U7snRNAs vectors targeting DMPK improve DM1 h..:

Almeida, Camila F. ; Robriquet, Florence ; Vetter, Tatyana A....
Frontiers in Cell and Developmental Biology.  11 (2023)  - p. , 2023
Link: https://doi.org/10.3389/..
 
?
5

Systemic PPMO-mediated dystrophin expression in the Dup2 mo..:

Gushchina, Liubov V. ; Vetter, Tatyana A. ; Frair, Emma C....
Molecular Therapy - Nucleic Acids.  30 (2022)  - p. 479-492 , 2022
Link: https://doi.org/10.1016/..
 
?
6

Emerging Perspectives on Gene Therapy Delivery for Neurodeg..:

Gomez Limia, Cintia ; Baird, Megan ; Schwartz, Maura...
Journal of Personalized Medicine.  12 (2022)  12 - p. 1979 , 2022
Link: https://doi.org/10.3390/..
 
?
7

Intron mutations and early transcription termination in Duc..:

Waldrop, Megan A. ; Moore, Steven A. ; Mathews, Katherine D....
Human Mutation.  43 (2022)  4 - p. 511-528 , 2022
Link: https://doi.org/10.1002/..
 
?
8

Systemic delivery of an AAV9 exon-skipping vector significa..:

Wein, Nicolas ; Vetter, Tatyana A. ; Vulin, Adeline...
Molecular Therapy - Methods & Clinical Development.  26 (2022)  - p. 279-293 , 2022
Link: https://doi.org/10.1016/..
 
?
9

Mechanisms of IRF2BPL-related disorders and identification ..:

Sinha Ray, Shrestha ; Dutta, Debdeep ; Dennys, Cassandra...
Cell Reports.  41 (2022)  10 - p. 111751 , 2022
Link: https://doi.org/10.1016/..
 
?
10

Performance Requirements of Membrane Reactors for the Appli..:

Dieterich, Vincent ; Wein, Nicolas ; Spliethoff, Hartmut.
Advanced Sustainable Systems.  6 (2022)  12 - p. , 2022
Link: https://doi.org/10.1002/..
 
?
11

Designed U7 snRNAs inhibit DUX4 expression and improve FSHD..:

Rashnonejad, Afrooz ; Amini-Chermahini, Gholamhossein ; Taylor, Noah K...
Molecular Therapy - Nucleic Acids.  23 (2021)  - p. 476-486 , 2021
Link: https://doi.org/10.1016/..
 
?
12

Pre-clinical dose-escalation studies establish a therapeuti..:

Simmons, Tabatha R. ; Vetter, Tatyana A. ; Huang, Nianyuan...
Molecular Therapy - Methods & Clinical Development.  21 (2021)  - p. 325-340 , 2021
Link: https://doi.org/10.1016/..
 
?
13

Direct Reprogramming of Human Fibroblasts into Myoblasts to.. 

JoVE : Genetics
Almeida, Camila F. ; Frair, Emma C. ; Huang, Nianyuan... , 2021
Link: https://www.jove.com/t/6..
 
?
14

X-linked muscular dystrophy in a Labrador Retriever strain:..:

Barthélémy, Inès ; Calmels, Nadège ; Weiss, Robert B....
Skeletal Muscle.  10 (2020)  1 - p. , 2020
Link: https://doi.org/10.1186/..
 
?
15

Alternate Translational Initiation of Dystrophin: A Novel T..:

, In: Muscle Gene Therapy,
Wein, Nicolas ; Flanigan, Kevin M. - p. 371-382 , 2019
Link: https://doi.org/10.1007/..
 
1-15