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1 Ergebnisse
1
Specific DMPK-promoter targeting by CRISPRi reverses myoton..:
Porquet, Florent
;
Weidong, Lin
;
Jehasse, Kévin
...
info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtn.2023.05.007. , 2023
Link:
https://hal.science/hal-04287597
RT Journal T1
Specific DMPK-promoter targeting by CRISPRi reverses myotonic dystrophy type 1-associated defects in patient muscle cells
UL https://suche.suub.uni-bremen.de/peid=base-ftccsdartic:oai:HAL:hal-04287597v1&Exemplar=1&LAN=DE A1 Porquet, Florent A1 Weidong, Lin A1 Jehasse, Kévin A1 Gazon, Hélène A1 Kondili, Maria A1 Blacher, Silvia A1 Massotte, Laurent A1 Di Valentin, Emmannuel A1 Furling, Denis A1 Gillet, Nicolas, Albert A1 Klein, Arnaud, François A1 Seutin, Vincent A1 Willems, Luc PB HAL CCSD; Elsevier YR 2023 K1 Myotonic Dystrophy K1 gene therapy K1 CRISPRi K1 Cellular model K1 Dystrophie Mytotonique de type 1 K1 Thérapie génique K1 Modèles cellulaires K1 [SDV]Life Sciences [q-bio] K1 [SDV.BBM.BM]Life Sciences [q-bio]/Biochemistry K1 Molecular Biology/Molecular biology JF info:eu-repo/semantics/altIdentifier/doi/10.1016/j.omtn.2023.05.007 LK http://dx.doi.org/https://hal.science/hal-04287597 DO https://hal.science/hal-04287597 SF ELIB - SuUB Bremen
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